Disappointment and/or a glimmer of hope? - When biochemical efficacy does not translate into (primary) clinical benefit

Authors

Gere Sunder‐Plassmann (ORCID: https://orcid.org/0000-0002-9253-9921)
Christopher Paschen (ORCID: https://orcid.org/0000-0002-8456-0683)
Daniela Maria Allmer (ORCID: https://orcid.org/0009-0000-8060-0118)
Alice Schmidt (ORCID: https://orcid.org/0000-0002-5275-0044)

Institutions

Medical University of Vienna (AT)

Publication Details

Journal: Rare Disease and Orphan Drugs Journal
Published: 2026-10-30
DOI: https://doi.org/10.20517/rdodj.2026.32
Primary Topic: Statistical Methods in Clinical Trials
Type: article
Field-Weighted Citation Impact: 0.00

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article

Disappointment and/or a glimmer of hope? - When biochemical efficacy does not translate into (primary) clinical benefit

Gere Sunder‐Plassmann, Christopher Paschen, Daniela Maria Allmer, Alice Schmidt

Oct 30, 2026

3 links

Rare Disease and Orphan Drugs Journal

Statistical Methods in Clinical Trials

article

Disappointment and/or a glimmer of hope? - When biochemical efficacy does not translate into (primary) clinical benefit

Gere Sunder‐Plassmann, Christopher Paschen, Daniela Maria Allmer, Alice Schmidt

October 30, 2026article en

Abstract

No abstract available for this paper.

Rare Disease and Orphan Drugs JournalVol. 5(4)

Medical University of Vienna (AT)

Good health and well-being

Openalex Percentile: Top 12%

Statistical Methods in Clinical Trials

DOI Open Access PDF OpenAlex

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Disappointment and/or a glimmer of hope? - When biochemical efficacy does not translate into (primary) clinical benefit — Gere Sunder‐Plassmann, Christopher Paschen, et al. · Rare Disease and Orphan Drugs Journal (2026) | TGRS Research Map | TGRS