Is hematopoietic stem cell transplantation indicated in THPO-mutated congenital amegakaryocytic thrombocytopenia? Comment on: "Avatrombopag as a novel salvage therapy for refractory thrombocytopenia in THPO-mutated congenital amegakaryocytic thromboc
Authors
- Paul Saultier (ORCID: https://orcid.org/0000-0002-6327-0898)
- Alessandro Pecci (ORCID: https://orcid.org/0000-0001-9202-7013)
Institutions
- Aix-Marseille Université (FR)
- University of Pavia (IT)
Publication Details
- Journal
- Haematologica
- Published
- 2026-10-15
- DOI
- https://doi.org/10.3324/haematol.2026.302090
- Primary Topic
- Platelet Disorders and Treatments
- Type
- article
- Field-Weighted Citation Impact
- 0.00