Genotype and Ultrastructure Correlation in Primary Ciliary Dyskinesia Among Saudi Children: A Case Series
Background: Primary ciliary dyskinesia (PCD) is a rare inherited disorder of motile cilia causing chronic oto-sinopulmonary disease. Transmission electron microscopy (TEM) remains essential for confirming ultrastructural defects, especially in resource-limited settings. This study characterizes the clinicopathologic and molecular spectrum of Saudi children with PCD. Methods: Ten Saudi children with confirmed PCD (2018–2025) were retrospectively reviewed. Clinical, radiological, ultrastructural, and whole exome sequencing (WES) data were analyzed to assess genotype–phenotype correlation. Results: The cohort included seven females and three males (median age 9 years). Consanguinity was present in 80%, and five had situs inversus. TEM showed class 1 defects in 3 patients, class 2 in 2, and abnormalities of uncertain significance in 3. WES identified variants in DNAAF3, DNAAF4, RSPH9, GAS2L2, and NME5. Conclusions: This study expands the molecular and ultrastructural profile of PCD in Saudi Arabia. TEM remains essential for diagnosis and variant interpretation.
Authors
- Wajd A. Althakfi
Institutions
- King Saud Medical City (SA)
- King Saud University (SA)
Publication Details
- Journal
- Fetal and Pediatric Pathology
- Published
- 2026-07-30
- DOI
- https://doi.org/10.1080/15513815.2026.2699115
- Primary Topic
- Cystic Fibrosis Research Advances
- Type
- article
- Field-Weighted Citation Impact
- 0.00