Defining the therapeutic corridor of stability in enzyme replacement therapy for Pompe disease: a position statement
Authors
- Benedikt G. H. Schoser (ORCID: https://orcid.org/0000-0002-2757-8131)
Publication Details
- Journal
- Orphanet Journal of Rare Diseases
- Published
- 2026-07-28
- DOI
- https://doi.org/10.1186/s13023-026-04518-9
- Primary Topic
- Lysosomal Storage Disorders Research
- Type
- article
- Field-Weighted Citation Impact
- 0.00