Risks and benefits of gene therapy and transplantation in sickle cell disease. Comment on: ,HLA-haploidentical hematopoietic stem cell transplantation in patients with sickle cell disease: results from the phase II DREP-HAPLO trial-
Authors
- Haydar Frangoul
- Mariane De Montalembert
Institutions
- Inserm (FR)
- Assistance Publique – Hôpitaux de Paris (FR)
- Children’s Hospital at TriStar Centennial (US)
Publication Details
- Journal
- Haematologica
- Published
- 2026-07-23
- DOI
- https://doi.org/10.3324/haematol.2026.301370
- Primary Topic
- Hemoglobinopathies and Related Disorders
- Type
- article
- Field-Weighted Citation Impact
- 0.00
Funders
- Vertex Pharmaceuticals
- Jazz Pharmaceuticals