Leucovorin for Cerebral Folate Deficiency
The FDA has approved use of oral leucovorin calcium (folinic acid) for treatment of cerebral folate transport deficiency in patients who have a confirmed variant in the folate receptor 1 gene (FOLR1-CFTD). It is the first drug to be approved for this extremely rare disorder.
Publication Details
- Journal
- The medical letter on drugs and therapeutics/The medical letter
- Published
- 2026-05-11
- DOI
- https://doi.org/10.58347/tml.2026.1754b
- Primary Topic
- Folate and B Vitamins Research
- Type
- article
- Field-Weighted Citation Impact
- 0.00