Designed Minibinders Rewire Receptor Signaling to Enable Functional Human Myogenic Reprogramming
Sarcopenia, loss of muscle mass is a considerable health burden that demands immediate societal attention. Direct myogenic somatic cell reprogramming, a potential muscle regeneration method is constrained by an inability to control the signaling logic that governs cell fate. Here, we show that this barrier can be overcome using AI-designed receptor modulators. Screening de novo minibinders, we identify a synthetic protein cocktail, C6-DPC, that drives efficient human fibroblast-to-muscle transdifferentiation with robust structural and metabolic maturation. C6-DPC reprograms extracellular signaling by activating pro-myogenic FGFR1/2c pathways while suppressing anti-myogenic inputs through ALK1 and TGFBR2; targeted depletion of ALK1 is sufficient to lower the reprogramming barrier. Inflammatory signaling via gp130 emerges as a dominant checkpoint, and its inhibition further enhances conversion. Engineered tissues generate high twitch and tetanic forces in both wild-type and dystrophin-deficient human cells. These findings demonstrate that programmable synthetic ligands can rewrite receptor-level signaling to direct cell fate and enable functional tissue regeneration.
Authors
- David L. Mack (ORCID: https://orcid.org/0000-0003-1340-7056)
- Julie Mathieu (ORCID: https://orcid.org/0000-0002-3826-3549)
- Hannele Ruohola‐Baker (ORCID: https://orcid.org/0000-0002-5588-4531)
- Riya Keshri (ORCID: https://orcid.org/0000-0001-7708-6402)
- David A. Baker (ORCID: https://orcid.org/0000-0001-7896-6217)
- Alec S.T. Smith (ORCID: https://orcid.org/0000-0002-0001-8484)
- Marc Expòsit (ORCID: https://orcid.org/0000-0002-2980-303X)
- Sanjay Srivatsan (ORCID: https://orcid.org/0000-0001-7282-0487)
- Philip Barrett (ORCID: https://orcid.org/0000-0003-3963-4601)
- David Lee (ORCID: https://orcid.org/0000-0002-7536-9692)
- Alexander Robinson (ORCID: https://orcid.org/0000-0002-6800-4070)
- Aditya Krishnakumar (ORCID: https://orcid.org/0000-0003-3461-0133)
- Zachary Foreman
- Mohamad Abedi
- Shruti Jain
- Xinru Wang
- Melodie Chiu
- Gabriela Reyes
- Ethan Narog
- Jay Shendure
- Ashish A. Phal
Institutions
- Howard Hughes Medical Institute (US)
- University of Washington (US)
- ID Genomics (United States) (US)
- Protein Research Foundation (JP)
- Seattle University (US)
Publication Details
- Journal
- bioRxiv (Cold Spring Harbor Laboratory)
- Published
- 2026-04-27
- DOI
- https://doi.org/10.64898/2026.04.26.720818
- Primary Topic
- Muscle Physiology and Disorders
- Type
- article
- Field-Weighted Citation Impact
- 0.00