Estimating the Impact of Hemophilia A Treatment Administration on Patient Health Utility: Combining a Discrete Choice Experiment with Time Trade-Off Method
All coreHEM outcomes are important for treatment choices of PWHA. One-time IV infusion with 5- to 10-year durability can provide important patient utility gains over lifelong repeated SQ injections or IV infusions.
Institutions
- Tulane University (US)
- University of Washington (US)
- Impact (CA)
- BioMarin (United States) (US)
- McMaster University (CA)
Publication Details
- Journal
- Advances in Therapy
- Published
- 2026-03-24
- DOI
- https://doi.org/10.1007/s12325-026-03556-w
- Primary Topic
- Hemophilia Treatment and Research
- Type
- article
- Field-Weighted Citation Impact
- 0.00