450P Proteogenomics refines the molecular classification of leptomeningeal metastases in EGFR+ NSCLC
Background: Dato-DXd, a TROP2-directed antibody-drug conjugate, has shown efficacy in patients with EGFRm NSCLC.Elucidating the biological basis could clarify the molecular features that regulate Dato-DXd anti-tumor efficacy.We investigated Dato-DXd and DXd sensitivity biomarkers and impact of prior osimertinib treatment in preclinical models of NSCLC. Methods:In vitro viability screening performed in non-squamous (NSQ) and squamous (SQ) NSCLC cell lines (n=58) including 7 EGFRm cell lines.Internalization assays performed via live-cell imaging after osimertinib pre-treatment in EGFRm cell lines.In vivo studies evaluated single-dose Dato-DXd (10 mg/kg) in NSCLC patient-derived xenografts (PDX) models (n=38, including 15 EGFRm).Results: Dato-DXd activity was observed in EGFRwt (10/36 responders (R), 28%) and EGFRm (3/7 R, 43%) NSQ NSCLC cell lines.In this panel of models, SQ EGFRwt cell lines showed limited sensitivity to Dato-DXd (1/15 R, 7%).In addition, Dato-DXd demonstrated broader activity in EGFRm (11/15 R, 73%) compared to EGFRwt (11/23 R, 48%) NSCLC PDX models.Dato-DXd efficacy was observed in classical and atypical EGFRm PDX models.Mechanistically, TROP2 gene expression was necessary, but not sufficient for Dato-DXd response, suggesting additional biological factors are important.A NRF2 pathway signature and ABCC1 gene expression, putative DXd resistance markers, were associated with lower sensitivity to DXd and Dato-DXd.Interestingly, these were less prevalent in EGFRm compared to EGFRwt models, providing further preclinical rationale regarding the differential sensitivity of EGFRm tumors.Importantly, data also indicated the potential of osimertinib pre-treatment to enhance TROP2 expression and Dato-DXd internalization in EGFRm models.Conclusions: These preclinical data support the notable clinical activity of Dato-DXd in EGFRm NSCLC and provide a potential mechanistic rationale for why EGFRm disease has broad inherent sensitivity to Dato-DXd.Further validation in clinical cohorts is warranted.
Authors
- Yanan Li (ORCID: https://orcid.org/0000-0002-1868-3626)
- C-C. Li
- Shan Gao (ORCID: https://orcid.org/0000-0003-1950-0729)
- Sen Lin (ORCID: https://orcid.org/0000-0002-0367-7434)
- Y. Wu (ORCID: https://orcid.org/0000-0002-1528-4865)
- Y. Pan
- K. Yin
- G. Wang
- C.C. Wong
- P. Li
- M. Zheng
- H. Chen
- H. Tu
- X. Zhang
- Q. Zhou
- W-Z. Zhong
- L-B. Tang
- X-R. Sun
Institutions
- Chinese Academy of Sciences (CN)
- Chinese Academy of Medical Sciences & Peking Union Medical College (CN)
- Guangzhou Institutes of Biomedicine and Health (CN)
- Burning Rock Biotech (China) (CN)
- Guangdong Academy of Medical Sciences (CN)
- Guangdong Provincial People's Hospital (CN)
Publication Details
- Journal
- ESMO Open
- Published
- 2026-03-17
- DOI
- https://doi.org/10.1016/j.esmoop.2026.106764
- Primary Topic
- Brain Metastases and Treatment
- Type
- article
- Field-Weighted Citation Impact
- 0.00