The global impact of imiglucerase therapy in children with Gaucher disease types 1 and 3: a real-world analysis from the International Collaborative Gaucher Group Gaucher Registry
Authors
Jenny L. Carwile (ORCID: https://orcid.org/0000-0002-7229-5712)
Maria G. Perichon (ORCID: https://orcid.org/0009-0003-9803-6385)
The global impact of imiglucerase therapy in children with Gaucher disease types 1 and 3: a real-world analysis from the International Collaborative Gaucher Group Gaucher Registry
Jenny L. Carwile, Maria G. Perichon, Isabela Batsu, Azza Abdel Gawad Tantawy et al.
Journal
Orphanet Journal of Rare Diseases
Topics
Lysosomal Storage Disorders Research
article
The global impact of imiglucerase therapy in children with Gaucher disease types 1 and 3: a real-world analysis from the International Collaborative Gaucher Group Gaucher Registry
Jenny L. Carwile, Maria G. Perichon, Isabela Batsu, Azza Abdel Gawad Tantawy, Thomas Andrew Burrow, Jaya Ganesh, Julie L. Batista, Antonio Oliveira-dos-Santos, Jose Simon Camelo, Pramod K. Mistry
article en
Abstract
No abstract available for this paper.
Publication Tag
Orphanet Journal of Rare Diseases
Institutions
Ain Shams University (EG), Arkansas Children's Hospital (US), Universidade de São Paulo (BR), Yale University (US), Interventional Orthopedics Foundation (US), Sanofi (United States) (US), Sanofi (Brazil) (BR), University of Arkansas for Medical Sciences (US), Icahn School of Medicine at Mount Sinai (US)