Outcomes of hematopoietic stem cell transplantation for pediatric patients with transfusion-dependent thalassemia in Thailand

Our results broaden the donor pool by demonstrating comparable outcomes between MRD and MUD transplantation. Optimizing pretransplant care, such as regular pre-HSCT transfusion, adjusting conditioning intensity, and improving posttransplant supportive care, may mitigate age-related risks in older recipients.

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Publication Details

Journal
Clinical and Experimental Pediatrics
Published
2026-03-13
DOI
https://doi.org/10.3345/cep.2025.02173
Primary Topic
Hemoglobinopathies and Related Disorders
Type
article
Field-Weighted Citation Impact
0.00

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article

Outcomes of hematopoietic stem cell transplantation for pediatric patients with transfusion-dependent thalassemia in Thailand

Samart Pakakasama, Bunchoo Pongtanakul, Piya Rujkijyanont, Nongnuch Sirachainan et al.
Clinical and Experimental Pediatrics
Hemoglobinopathies and Related Disorders
article

Outcomes of hematopoietic stem cell transplantation for pediatric patients with transfusion-dependent thalassemia in Thailand

Samart Pakakasama, Bunchoo Pongtanakul, Piya Rujkijyanont, Nongnuch Sirachainan, Kamala Laohverapanich, Supanun Lauhasurayotin, Nattee Narkbunnam, Suradej Hongeng, Kleebsabai Sanpakit, Pornpun Sripornsawan, Thirachit Chotsampancharoen, Chayamon Takpradit, Duantida Songdej, Usanarat Anurathapan, Kanhatai Chiengthong
article en

Abstract

Our results broaden the donor pool by demonstrating comparable outcomes between MRD and MUD transplantation. Optimizing pretransplant care, such as regular pre-HSCT transfusion, adjusting conditioning intensity, and improving posttransplant supportive care, may mitigate age-related risks in older recipients.

Clinical and Experimental Pediatrics
Prince of Songkla University (TH), Siriraj Hospital (TH), Chulalongkorn University (TH), Mahidol University (TH), Phramongkutklao Hospital (TH), Ramathibodi Hospital (TH), Phramongkutklao College of Medicine
Mahidol University, Faculty of Medicine Siriraj Hospital, Mahidol University
Good health and well-being
Openalex Percentile: Top 26%
Hemoglobinopathies and Related Disorders
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