Outcomes of hematopoietic stem cell transplantation for pediatric patients with transfusion-dependent thalassemia in Thailand
Our results broaden the donor pool by demonstrating comparable outcomes between MRD and MUD transplantation. Optimizing pretransplant care, such as regular pre-HSCT transfusion, adjusting conditioning intensity, and improving posttransplant supportive care, may mitigate age-related risks in older recipients.
Authors
- Samart Pakakasama (ORCID: https://orcid.org/0000-0001-8118-163X)
- Bunchoo Pongtanakul (ORCID: https://orcid.org/0000-0003-4204-0118)
- Piya Rujkijyanont (ORCID: https://orcid.org/0000-0002-5006-9810)
- Nongnuch Sirachainan (ORCID: https://orcid.org/0000-0001-8039-5476)
- Kamala Laohverapanich (ORCID: https://orcid.org/0000-0001-6444-3677)
- Supanun Lauhasurayotin (ORCID: https://orcid.org/0000-0002-2432-8022)
- Nattee Narkbunnam
- Suradej Hongeng (ORCID: https://orcid.org/0000-0002-7376-9393)
- Kleebsabai Sanpakit (ORCID: https://orcid.org/0000-0003-3452-1894)
- Pornpun Sripornsawan (ORCID: https://orcid.org/0000-0001-5130-0714)
- Thirachit Chotsampancharoen (ORCID: https://orcid.org/0000-0002-0111-6318)
- Chayamon Takpradit (ORCID: https://orcid.org/0000-0002-3723-4543)
- Duantida Songdej
- Usanarat Anurathapan
- Kanhatai Chiengthong
Institutions
- Prince of Songkla University (TH)
- Siriraj Hospital (TH)
- Chulalongkorn University (TH)
- Mahidol University (TH)
- Phramongkutklao Hospital (TH)
- Ramathibodi Hospital (TH)
- Phramongkutklao College of Medicine
Publication Details
- Journal
- Clinical and Experimental Pediatrics
- Published
- 2026-03-13
- DOI
- https://doi.org/10.3345/cep.2025.02173
- Primary Topic
- Hemoglobinopathies and Related Disorders
- Type
- article
- Field-Weighted Citation Impact
- 0.00
Funders
- Mahidol University
- Faculty of Medicine Siriraj Hospital, Mahidol University