Preclinical assessment of GNE <sup>wt</sup> /bi-shRNA-GNE <sup>M743T</sup> lipoplex product development for GNE myopathy
These results encourage future studies, potentially leading toward clinical testing of GNE<sup>wt</sup>/bi-shRNA-GNE<sup>M743T</sup> lipoplex for GNE myopathy.
Authors
- Ernest Bognar (ORCID: https://orcid.org/0000-0003-0314-7529)
- Fabienne Kerneis
- Christopher M. Jay
- Laura Stanbery (ORCID: https://orcid.org/0000-0001-7251-4076)
- Alexander Nemunaitis
- Donald D. Rao
- Jeremy Winchester
- Sep Sarshar
- Emily Nemunaitis
- Adam Walter
- John Nemunaitis
Institutions
- Ecologie fonctionnelle & biogéochimie des sols & des agro-systèmes (FR)
- Gradalis (United States) (US)
- Taylor Wimpey (United Kingdom) (GB)
Publication Details
- Journal
- Future Science OA
- Published
- 2026-03-02
- DOI
- https://doi.org/10.1080/20565623.2026.2635722
- Primary Topic
- Inflammatory Myopathies and Dermatomyositis
- Type
- article
- Field-Weighted Citation Impact
- 0.00