Hematopoietic Stem Cell Transplantation for CSF1R-Related Disorder: A Longitudinal Study of Efficacy and Safety
HSCT is a potent disease-modifying therapy for CSF1R-RD, drastically improving survival and slowing deterioration. The findings underscore the necessity of early intervention during the symptomatic phase to maximize the preservation of quality of life for affected individuals.
Authors
- Audrey Strongosky (ORCID: https://orcid.org/0000-0003-4734-0339)
- Patrycja Mensah-Glanowska
- Tomasz Tomasz
- Zbigniew K. Wszolek
- Ernesto Ayala
- Kamila Żur-Wyrozumska
- Erik H. Middlebrooks
Institutions
- Jagiellonian University (PL)
- Medical University of Silesia (PL)
- Military Hospital (PK)
- Jacksonville College (US)
- 1 Military Clinical Hospital with Outpatient Clinic (PL)
- Mayo Clinic in Florida (US)
Publication Details
- Journal
- Journal of Movement Disorders
- Published
- 2026-02-27
- DOI
- https://doi.org/10.14802/jmd.26005
- Primary Topic
- Acute Myeloid Leukemia Research
- Type
- article
- Field-Weighted Citation Impact
- 0.00