Real-World Outcomes and Toxicities of CAR-T in Relapsed/Refractory Follicular Lymphoma: A Multicenter Cohort Study
Chimeric antigen receptor T-cell (CAR-T) therapy revolutionized treatment of relapsed/refractory (R/R) follicular lymphoma (FL). Real-world efficacy and toxicity data are needed as clinical trial populations are often not representative. Hence, we conducted a multi-center retrospective study of patients with R/R FL undergoing commercial CAR-T with axicabtagene ciloleucel (axi-cel) or tisagenlecleucel (tisa-cel) between 2021 and 2024. Endpoints included measures of efficacy (overall response rate [ORR], complete response rate [CRR], progression-free survival [PFS], and overall survival [OS]) and toxicity (rates of cytokine release syndrome [CRS] and immune effector cell-associated neurotoxicity syndrome [ICANS]). Among 136 patients, 100 (74%) received axi-cel and 36 (26%) received tisa-cel. Axi-cel patients were younger (median age 60 vs 68 years, p=0.001) and received bendamustine lymphodepletion less often (9% vs 33%, p<0.001). Median follow up was 14.4 months (range 0.8 - 72.0 months). In the unweighted analysis, axi-cel was associated with higher ORR (96% vs 80%, p=0.007), CRR (88% vs 71%, p=0.024), and longer median PFS (30.5 months vs 11.9 months, p=0.021) compared with tisa-cel. Median OS did not differ significantly between the two products (not reached vs 23.6 months, p=0.061). Rates of CRS were comparable (75% vs 75%, p=0.99), whereas ICANS occurred more frequently with axi-cel (42% vs 17%, p=0.008). After inverse probability of treatment weighting, efficacy outcomes were largely similar between axi-cel and tisa-cel, however, axi-cel remained associated with significantly higher toxicity. In real-world settings, both axi-cel and tisa-cel demonstrated efficacy in patients with R/R FL, although PFS was inferior to that reported in clinical trials.
Authors
- Geoffrey Shouse (ORCID: https://orcid.org/0000-0002-7917-5713)
- John Graham Sharp (ORCID: https://orcid.org/0000-0003-3023-8063)
- Ari Pelcovits (ORCID: https://orcid.org/0000-0002-3354-4499)
- Lindsey A. Fitzgerald (ORCID: https://orcid.org/0000-0001-5988-2878)
- Andinet Teferra
- John S. Wang (ORCID: https://orcid.org/0000-0002-7191-0437)
- Victor Yazbeck (ORCID: https://orcid.org/0000-0001-5113-8681)
- Timothy J. Voorhees (ORCID: https://orcid.org/0000-0001-7603-6454)
- Subodh Bhatta (ORCID: https://orcid.org/0000-0003-3804-5370)
- Joeseph Maakaron
- Catherine Reinert
- Reem Karmali
- Omar Elghawy
- Thomas A Ollila
- Colin J Thomas
- Andy I. Chen
- Daniel Reef
- William Bennett Clark
- Narendranath Epperla
- Alexey V Danilov
- Paolo Strati
- Sairah Ahmed
- Alexander Micah Gorzewski
- Jennifer J. Huang
- Natalie S. Grover
- Mazyar Shadman
- Manali Kamdar
- Esteban Toro Velez
Institutions
- Northwestern University (US)
- University of North Carolina at Chapel Hill (US)
- City Of Hope National Medical Center (US)
- The University of Texas MD Anderson Cancer Center (US)
- Oregon Health & Science University (US)
- Virginia Commonwealth University (US)
- University of Utah (US)
- Brown University (US)
- Hospital of the University of Pennsylvania (US)
- University of Minnesota System (US)
- Huntsman Cancer Institute (US)
- The Ohio State University Wexner Medical Center (US)
- Fred Hutch Cancer Center (US)
- Northwestern University (PH)
- City of Hope (US)
- University of Colorado Cancer Center (US)
- UNC Lineberger Comprehensive Cancer Center
- The Ohio State University (US)
- University of Pennsylvania (US)
- University of Colorado Denver (US)
Publication Details
- Journal
- Blood Advances
- Published
- 2026-02-26
- DOI
- https://doi.org/10.1182/bloodadvances.2025019115
- Primary Topic
- CAR-T cell therapy research
- Type
- article
- Field-Weighted Citation Impact
- 0.00
Funders
- Eli Lilly and Company
- AstraZeneca
- Gilead Sciences
- Regeneron Pharmaceuticals
- BeiGene
- Incyte
- Swedish Orphan Biovitrum
- Ipsen
- Genentech