Burden of disease in adult patients with hereditary angioedema: results from a multinational survey
Results of this large multinational survey highlight that patients included in this study, most of whom were not using first-line LTP, reported being burdened by their disease, including frequent HAE attacks, HRQoL impairment, poor disease control, and work productivity impairment.
Authors
- Ricardo Zwiener (ORCID: https://orcid.org/0000-0001-9636-6741)
- Mauricio Sarrazola
- Ryan Murphy (ORCID: https://orcid.org/0000-0003-1345-7723)
- Inmaculada Martinez‐Saguer
- Angela Simón
- Marie de la Cruz (ORCID: https://orcid.org/0000-0002-3343-8960)
- Maureen Watt
- Anete S. Grumach
Institutions
- Hospital Universitario Austral (AR)
- National Hemophilia Foundation (US)
- Takeda (United States) (US)
- Faculdade de Medicina do ABC (BR)
- University of Pamplona (CO)
Publication Details
- Journal
- Orphanet Journal of Rare Diseases
- Published
- 2026-02-19
- DOI
- https://doi.org/10.1186/s13023-025-04134-z
- Primary Topic
- Coagulation, Bradykinin, Polyphosphates, and Angioedema
- Type
- article
- Field-Weighted Citation Impact
- 0.00