Enzyme replacement therapy compared with best supportive care for the treatment of Pompe Disease: a systematic review and network meta-analysis
This article presents independent research funded by the National Institute for Health and Care Research (NIHR) Evidence Synthesis programme as award number NIHR161219.
Authors
- Chinyereugo Umemneku-Chikere (ORCID: https://orcid.org/0000-0003-4114-2227)
- Sarah J Nevitt (ORCID: https://orcid.org/0000-0001-9988-2709)
- Helen Fulbright (ORCID: https://orcid.org/0000-0002-1073-1099)
- M. Corbett
- Rachel Churchill (ORCID: https://orcid.org/0000-0002-1751-0512)
- Matthew Walton (ORCID: https://orcid.org/0000-0003-1932-3689)
- Nyanar Jasmine Deng (ORCID: https://orcid.org/0009-0006-5901-1101)
- Robin Lachmann
- Robert Hodgson
Institutions
- University College London Hospitals NHS Foundation Trust (GB)
- Cambridge University Hospitals NHS Foundation Trust (GB)
- National Hospital for Neurology and Neurosurgery (GB)
- University College London (GB)
- University of York (GB)
Publication Details
- Journal
- Health Technology Assessment
- Published
- 2025-07-30
- DOI
- https://doi.org/10.3310/gjrh0730
- Primary Topic
- Lysosomal Storage Disorders Research
- Type
- article
- Field-Weighted Citation Impact
- 0.00