Long-term growth hormone therapy improves adult height in children with Indian hedgehog (IHH)-related short stature
rhGH therapy was associated with clinically meaningful height gains, including adult height improvement, in children with IHH-related short stature; variant class may modify response.
Authors
- Cristine Barboza Beltrão
- Alexsandra C. Malaquias (ORCID: https://orcid.org/0000-0003-1514-0244)
- Mariana Ferreira de Assis Funari
- Ricardo Fernando Arrais (ORCID: https://orcid.org/0000-0002-9258-4263)
- Montenegro APDR
- Viviane Cassia Barrionuevo Jaime
- Laurana de Polli Cellin (ORCID: https://orcid.org/0009-0008-8097-8776)
- Amanda Latuffe Soares Damião
- Alexander Augusto de Lima Jorge
- Joaquim de Matos Cavalcante
- Ana Maria Santillan-Vasconez
- Renata da Cunha Scalco
- Leopoldo Digilio Vieira da Silva
Publication Details
- Journal
- Hormone Research in Paediatrics
- Published
- 2026-02-16
- DOI
- https://doi.org/10.1159/000551045
- Primary Topic
- Hedgehog Signaling Pathway Studies
- Type
- article
- Field-Weighted Citation Impact
- 0.00