First clinical experience with the Transthyretin Amyloidosis-Quality of Life questionnaire (ATTR-QoL): associations with clinical characteristics and established patient-reported outcomes
ATTR-QOL, as a disease-specific PRO, effectively captures the multidimensional impact of ATTR and is associated with clinical parameters and functionality in patients with ATTR.
Authors
- Karan Wats (ORCID: https://orcid.org/0000-0002-2488-9399)
- Andrew Lovley (ORCID: https://orcid.org/0000-0001-9118-0673)
- Sabrina Rebello (ORCID: https://orcid.org/0000-0002-0201-4030)
- Kaitlin LaGasse (ORCID: https://orcid.org/0000-0001-9772-5822)
- Alfonsina Mirabal Santos
- Juliana Levy
- Kristen Hsu
- D Bampatsias
- Mathew S Maurer
- Sergio Teruya
- Kristen L McCausland
- Phaedra T Johnson
Institutions
- NewYork–Presbyterian Hospital (US)
- Columbia University Irving Medical Center (US)
- IQVIA (United States) (US)
- Amyloidosis Foundation (US)
Publication Details
- Journal
- European Heart Journal - Quality of Care and Clinical Outcomes
- Published
- 2026-02-11
- DOI
- https://doi.org/10.1093/ehjqcco/qcag015
- Primary Topic
- Amyloidosis: Diagnosis, Treatment, Outcomes
- Type
- article
- Field-Weighted Citation Impact
- 0.00