Tofersen: A Novel Option for the Treatment of Amyotrophic Lateral Sclerosis
Tofersen provides a promising targeted treatment option for pathogenic SOD1 ALS. Ongoing studies will clarify its long-term clinical impact.
Authors
- Anna Nogid
- Michael Karros
- Marissa DiFulco
Institutions
- Fairleigh Dickinson University (US)
Publication Details
- Journal
- Annals of Pharmacotherapy
- Published
- 2026-02-04
- DOI
- https://doi.org/10.1177/10600280251408862
- Primary Topic
- Amyotrophic Lateral Sclerosis Research
- Type
- article
- Field-Weighted Citation Impact
- 0.00