An induced pluripotent stem cell-based chemical genetic approach for studying spinal muscular atrophy
Taken together, CMAP<sub>neuro</sub> represents a novel tool to identify candidate stimuli for follow-up investigation into the biology of SMA and related disorders.
Authors
- Richard M. Giadone (ORCID: https://orcid.org/0000-0003-4523-3062)
- Sabrina Ghosh (ORCID: https://orcid.org/0009-0003-0325-7346)
- Lee L. Rubin (ORCID: https://orcid.org/0000-0002-8658-841X)
- Kristina M. Holton (ORCID: https://orcid.org/0000-0002-1002-2882)
- Nicholas Lyons (ORCID: https://orcid.org/0000-0003-3921-106X)
- Aravind Subramanian (ORCID: https://orcid.org/0009-0006-5468-5916)
- Stanley P. Gill
- Xiaoyu Hu
- Ted Natoli
Institutions
- Broad Institute (US)
- Harvard University (US)
- Harvard Stem Cell Institute (US)
Publication Details
- Journal
- Frontiers in Neuroscience
- Published
- 2026-02-04
- DOI
- https://doi.org/10.3389/fnins.2025.1695359
- Primary Topic
- Neurogenetic and Muscular Disorders Research
- Type
- article
- Field-Weighted Citation Impact
- 0.00
Funders
- Broad Institute
- National Institutes of Health
- Harvard Stem Cell Institute
- Stanley Center for Psychiatric Research, Broad Institute