Electrophysiological Changes in Pediatric Spinal Muscular Atrophy: Results From an Observational Study
CMAP amplitudes can differentiate SMA disease severity and may increase after nusinersen treatment. Large-scale longitudinal studies are required to investigate CMAP amplitude as a biomarker of treatment response in patients with SMA.
Authors
- Jie Han (ORCID: https://orcid.org/0000-0001-9863-800X)
- Jun Jiang (ORCID: https://orcid.org/0000-0002-0063-3225)
- Jiajun Wu (ORCID: https://orcid.org/0009-0001-0139-799X)
- Xue Chen
- Dan Sun
- Xiaolong Deng
- Jing Wang
- Ruidi Sun
Institutions
- Tianjin Centers for Disease Control and Prevention (CN)
- Tianjin Children's Hospital (CN)
- Wuhan Children's Hospital (CN)
- Tianjin Medical University (CN)
Publication Details
- Journal
- Muscle & Nerve
- Published
- 2026-01-21
- DOI
- https://doi.org/10.1002/mus.70156
- Primary Topic
- Neurogenetic and Muscular Disorders Research
- Type
- article
- Field-Weighted Citation Impact
- 0.00