Electrophysiological Changes in Pediatric Spinal Muscular Atrophy: Results From an Observational Study

CMAP amplitudes can differentiate SMA disease severity and may increase after nusinersen treatment. Large-scale longitudinal studies are required to investigate CMAP amplitude as a biomarker of treatment response in patients with SMA.

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Publication Details

Journal
Muscle & Nerve
Published
2026-01-21
DOI
https://doi.org/10.1002/mus.70156
Primary Topic
Neurogenetic and Muscular Disorders Research
Type
article
Field-Weighted Citation Impact
0.00
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article

Electrophysiological Changes in Pediatric Spinal Muscular Atrophy: Results From an Observational Study

Jie Han, Jun Jiang, Jiajun Wu, Xue Chen et al.
Muscle & Nerve
Neurogenetic and Muscular Disorders Research
article

Electrophysiological Changes in Pediatric Spinal Muscular Atrophy: Results From an Observational Study

Jie Han, Jun Jiang, Jiajun Wu, Xue Chen, Dan Sun, Xiaolong Deng, Jing Wang, Ruidi Sun
article en

Abstract

CMAP amplitudes can differentiate SMA disease severity and may increase after nusinersen treatment. Large-scale longitudinal studies are required to investigate CMAP amplitude as a biomarker of treatment response in patients with SMA.

Muscle & Nerve
Tianjin Centers for Disease Control and Prevention (CN), Tianjin Children's Hospital (CN), Wuhan Children's Hospital (CN), Tianjin Medical University (CN)
Openalex Percentile: Top 81%
Neurogenetic and Muscular Disorders Research
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