Complement C5 Inhibitor Ameliorates a Case of Dysferlinopathy
Complement inhibition showed promising clinical improvement in this single case of dysferlinopathy. Further studies with larger sample sizes are needed to investigate the efficacy and safety of complement inhibitors in dysferlinopathy.
Authors
- Q. Edward Wang (ORCID: https://orcid.org/0009-0001-8333-2689)
- W. Zhang
- He Lv (ORCID: https://orcid.org/0000-0002-4148-625X)
- Meng Yu
- Yun Yuan
- Fuze Zheng
- Xin Lu
- Shuaikun Kang
Institutions
- Peking University (CN)
- National Health and Family Planning Commission (CN)
- Discovery Centre (CA)
- China-Japan Friendship Hospital (CN)
- Ministry of Education (ME)
- Peking University First Hospital (CN)
Publication Details
- Journal
- Neurology Neuroimmunology & Neuroinflammation
- Published
- 2026-01-13
- DOI
- https://doi.org/10.1212/nxi.0000000000200539
- Primary Topic
- Complement system in diseases
- Type
- article
- Field-Weighted Citation Impact
- 0.00