Pharmacoeconomic evaluation of spinal muscular atrophy therapy in patients with four SMN2 copies diagnosed through newborn screening
Presymptomatic SMA therapy in patients with four <i>SMN2</i> copies diagnosed through newborn screening reduces the total treatment costs over a 19-year horizon.
Authors
- A.S. Makarov
- LM Kuzenkova
- D. V. Vlodavets
- O.Yu. Germanenko
- N.A. Avxentyev
Institutions
- Sechenov University (RU)
- Pirogov Russian National Research Medical University (RU)
- Center for Children (US)
- Financial Research (Hungary) (HU)
- Sudan Meteorological Authority (SD)
Publication Details
- Journal
- S S Korsakov Journal of Neurology and Psychiatry
- Published
- 2025-12-30
- DOI
- https://doi.org/10.17116/jnevro2025125121188
- Primary Topic
- Neurogenetic and Muscular Disorders Research
- Type
- article
- Field-Weighted Citation Impact
- 0.00