Real-world clinical outcomes and treatment response in complement inhibitor experienced and naïve PNH patients prescribed pegcetacoplan in Europe and Canada
Pegcetacoplan proved effective for CI<sub>naïve</sub> and CI<sub>exp</sub> patients in a real-world setting, with numerically improved clinical outcomes and high response rate.
Authors
- Sam Williamson
- Juan Carlos Vallejo Llamas
- Jens Panse (ORCID: https://orcid.org/0000-0001-6316-3112)
- Koo K Wilson
- Zalmaï Hakimi (ORCID: https://orcid.org/0000-0001-5835-8599)
- Niall Hatchell (ORCID: https://orcid.org/0000-0002-8432-6379)
- Yasmin Taylor (ORCID: https://orcid.org/0000-0003-4454-5013)
- Barbara Czech
- Brianne Kerr
- Christopher J. Patriquin
Institutions
- University Health Network (CA)
- Universidad de Salamanca (ES)
- Health Net (US)
- Adelphi Group (United Kingdom) (GB)
- RWTH Aachen University (DE)
Publication Details
- Journal
- Hematology
- Published
- 2026-01-02
- DOI
- https://doi.org/10.1080/16078454.2025.2608510
- Primary Topic
- Complement system in diseases
- Type
- article
- Field-Weighted Citation Impact
- 0.00