Quinazolinone and Phthalazinone Inhibitors of the HDAC6/Ubiquitin Protein-Protein Interaction
Histone deacetylase 6 (HDAC6) is a class IIb histone deacetylase that regulates diverse cytosolic acetylation through its two catalytic deacetylase domains and a C-terminal zinc finger ubiquitin-binding domain (ZnF-UBD) which mediates key protein-protein interactions (PPIs) that couple deacetylation and ubiquitin-dependent degradation. While most HDAC6 inhibitors target the catalytic domains, the ZnF-UBD represents an underexplored target. Here, we report the development of small-molecule inhibitors of the HDAC6 ZnF-UBD/ubiquitin interaction based on quinazolinone and phthalazinone scaffolds. Starting from known quinazolinone inhibitors, a modeling-guided scaffold hop revealed a novel phthalazinone series and late-stage diversification yield compounds with improved predicted physicochemical properties. Furthermore, machine-learning-based co-folding affinity predictions reproduced experimental IC rank order, highlighting their utility in PPI inhibitor design. These studies expand the chemical space of HDAC6 ZnF-UBD inhibitors and provide a foundation for future therapeutic and mechanistic exploration of HDAC6-ubiquitin signaling.
Authors
- Sydney Gordon
- George M. Burslem (ORCID: https://orcid.org/0000-0002-2812-983X)
- Callie E. W. Crawford (ORCID: https://orcid.org/0009-0008-9600-815X)
- Jordi C. J. Hintzen (ORCID: https://orcid.org/0000-0002-4621-0711)
- Sebastian Dilones
Institutions
- Translational Therapeutics (United States) (US)
- University of Pennsylvania (US)
Publication Details
- Journal
- bioRxiv (Cold Spring Harbor Laboratory)
- Published
- 2025-12-20
- DOI
- https://doi.org/10.64898/2025.12.18.695271
- Primary Topic
- Histone Deacetylase Inhibitors Research
- Type
- article
- Field-Weighted Citation Impact
- 0.00
Funders
- University of Pennsylvania
- National Institutes of Health
- National Institute of General Medical Sciences