2nd NMD4C basic research summer school on promoting standardized protocols to advance translational research in neuromuscular disorders
The Neuromuscular Disease Network for Canada aims to accelerate research and improve care for individuals living with neuromuscular disorders by connecting basic scientists, clinicians, and trainees nationwide. As part of this mission, the network held its second Basic Research Summer School (May 7-8, 2025, York University, Toronto), integrating patient and caregiver perspectives with advanced scientific sessions and full-day methodological workshops. The program emphasized experimental rigor, reproducibility, and collaboration across research pillars, while launching the Basic Science Trainee Committee and Canada's first national, publicly accessible database of standard operating procedures for muscle research. This trainee-led, reproducibility-focused model of Summer School provides a transferable framework for building standardized preclinical capacity across international neuromuscular disorders research networks.
Authors
- Homira Osman (ORCID: https://orcid.org/0009-0001-4225-9075)
- Rashmi Kothary (ORCID: https://orcid.org/0000-0002-9239-7310)
- J. K. Lee
- Jean‐Philippe Leduc‐Gaudet (ORCID: https://orcid.org/0000-0002-7637-5445)
- Natasha C. Chang (ORCID: https://orcid.org/0000-0003-0589-9660)
- Anthony Scimè (ORCID: https://orcid.org/0000-0002-7128-4384)
- Luke D. Flewwelling
- Kim Patten
- Madison C. Garibotti
- Christopher G. R. Perry (ORCID: https://orcid.org/0000-0002-5745-5888)
- Arthur J. Cheng (ORCID: https://orcid.org/0000-0003-3862-2967)
- Adrien Rihoux (ORCID: https://orcid.org/0000-0002-6974-5022)
- Emma R Sutton (ORCID: https://orcid.org/0009-0002-2127-6850)
Institutions
- University of Ottawa (CA)
- York University (CA)
- Muscular Dystrophy Canada (CA)
- Ottawa Hospital (CA)
- Armand Frappier Museum (CA)
- Ottawa Hospital Research Institute (CA)
- McGill University (CA)
- Université du Québec à Trois-Rivières (CA)
- Université de Montréal (CA)
Publication Details
- Journal
- Journal of Neuromuscular Diseases
- Published
- 2025-12-19
- DOI
- https://doi.org/10.1177/22143602251408154
- Primary Topic
- Muscle Physiology and Disorders
- Type
- article
- Field-Weighted Citation Impact
- 0.00