Real-world evidence of Nusinersen treatment for patients with spinal muscular atrophy in the Kingdom of Saudi Arabia
The study demonstrates that baseline and follow-up data from multiple motor and functional assessment scales were essential for evaluating disease progression and treatment response in SMA.
Authors
- Hajer Almudaiheem (ORCID: https://orcid.org/0000-0002-0985-6193)
- Fowzia Ibrahim (ORCID: https://orcid.org/0000-0002-7069-8024)
- Fahad A. Bashiri (ORCID: https://orcid.org/0000-0003-1436-6727)
- Fouad Alghamdi
- Ahmed Al‐Jedai (ORCID: https://orcid.org/0000-0002-4730-9086)
- Tareef Alaama (ORCID: https://orcid.org/0000-0002-9362-0182)
- Abdulaziz Alsaman
- Aljohara A Alsakran
- Mohammed Abdelrahman Almuhaizae
- Eman Ahmed Yousef Matter
Institutions
- King Faisal University (SA)
Publication Details
- Journal
- Saudi Medical Journal
- Published
- 2025-12-01
- DOI
- https://doi.org/10.15537/smj.2025.46.12.20250107
- Primary Topic
- Neurogenetic and Muscular Disorders Research
- Type
- article
- Field-Weighted Citation Impact
- 0.00