A Psychometric Evaluation of Maximum Phonation Time and <scp> <i>S</i> / <i>Z</i> </scp> Ratio as Pragmatic Outcome Measures of Bulbar Function in Adults With Spinal Muscular Atrophy
MPT is a low-cost pragmatic tool to measure bulbar function and a surrogate for respiratory function OMs among awSMA. MPT may be helpful for patients with limited access to alternative bulbar or respiratory measures or for telehealth clinical care settings. MPT's low sensitivity to change limits its clinical utility over a 12-month interval. Larger studies are necessary.
Authors
- Colleen O’Connell (ORCID: https://orcid.org/0000-0002-4760-4093)
- Shane McCullum
- Jeremy Slayter (ORCID: https://orcid.org/0000-0002-1048-266X)
- Dick Drost
- Lauren Casey (ORCID: https://orcid.org/0000-0003-2897-3210)
- Anne Christie
Institutions
- Dalhousie University (CA)
- Saint John Regional Hospital (CA)
- Horizon Health Network (CA)
Publication Details
- Journal
- Muscle & Nerve
- Published
- 2025-12-12
- DOI
- https://doi.org/10.1002/mus.70104
- Primary Topic
- Shoulder Injury and Treatment
- Type
- article
- Field-Weighted Citation Impact
- 0.00
Funders
- F. Hoffmann-La Roche
- Fondation de la recherche en santé du Nouveau-Brunswick
- Dalhousie University
- Faculty of Medicine, Dalhousie University