Pegcetacoplan in idiopathic and familial pediatric C3 glomerulopathy

These findings support the potential of C3 inhibition with pegcetacoplan in pediatric patients with refractory or genetic C3G.

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Publication Details

Journal
Pediatric Nephrology
Published
2025-12-08
DOI
https://doi.org/10.1007/s00467-025-07092-7
Primary Topic
Complement system in diseases
Type
article
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article

Pegcetacoplan in idiopathic and familial pediatric C3 glomerulopathy

Marina Sáez Belló, Pilar Llopis Salvià, Mónica Climente Martí, Santiago Rodrı́guez de Córdoba et al.
Pediatric Nephrology
Complement system in diseases
article

Pegcetacoplan in idiopathic and familial pediatric C3 glomerulopathy

Marina Sáez Belló, Pilar Llopis Salvià, Mónica Climente Martí, Santiago Rodrı́guez de Córdoba, Elena Román Ortiz, Francisco Aguilar Bacallado, Andrea Reparaz Suevos, Marisa Perez Ebri
article en

Abstract

These findings support the potential of C3 inhibition with pegcetacoplan in pediatric patients with refractory or genetic C3G.

Pediatric NephrologyVol. 41(5)
Fundación para el Fomento de la Investigación Sanitaria y Biomédica de la Comunitat Valenciana (ES), Hospital Universitario Doctor Peset (ES), Hospital General Universitario De Valencia (ES), Centro de Investigaciones Biológicas Margarita Salas (ES)
Openalex Percentile: Top 55%
Complement system in diseases
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