Pegcetacoplan in idiopathic and familial pediatric C3 glomerulopathy
These findings support the potential of C3 inhibition with pegcetacoplan in pediatric patients with refractory or genetic C3G.
Authors
- Marina Sáez Belló
- Pilar Llopis Salvià
- Mónica Climente Martí (ORCID: https://orcid.org/0000-0002-4387-1987)
- Santiago Rodrı́guez de Córdoba (ORCID: https://orcid.org/0000-0001-6401-1874)
- Elena Román Ortiz (ORCID: https://orcid.org/0000-0003-4942-3883)
- Francisco Aguilar Bacallado
- Andrea Reparaz Suevos
- Marisa Perez Ebri
Institutions
- Fundación para el Fomento de la Investigación Sanitaria y Biomédica de la Comunitat Valenciana (ES)
- Hospital Universitario Doctor Peset (ES)
- Hospital General Universitario De Valencia (ES)
- Centro de Investigaciones Biológicas Margarita Salas (ES)
Publication Details
- Journal
- Pediatric Nephrology
- Published
- 2025-12-08
- DOI
- https://doi.org/10.1007/s00467-025-07092-7
- Primary Topic
- Complement system in diseases
- Type
- article
- Field-Weighted Citation Impact
- 0.00