Identification and Estimation of Vaccine Effectiveness in the Test-Negative Design Under Equi-confounding
The test-negative design (TND) is widely used to evaluate vaccine effectiveness in real-world settings. In a TND study, individuals with similar symptoms who seek care are tested, and effectiveness is estimated by comparing vaccination histories of test-positive cases and test-negative controls. The TND is often justified on the grounds that it reduces confounding due to unmeasured health-seeking behavior, although this has not been formally described using potential outcomes. At the same time, concerns persist that conditioning on test receipt can introduce selection bias. We provide a formal justification of the TND under an assumption of odds ratio equi-confounding, where unmeasured confounders affect test-positive and test-negative individuals equivalently on the odds ratio scale. Health-seeking behavior is one plausible example. We also show that these results hold under the outcome-dependent sampling used in TNDs. We discuss the design implications of the equi-confounding assumption and provide alternative estimators for the marginal risk ratio among the vaccinated under equi-confounding, including outcome modeling and inverse probability weighting estimators as well as a semiparametric estimator that is doubly robust. When equi-confounding does not hold, we suggest a straightforward sensitivity analysis that parameterizes the magnitude of the deviation on the odds ratio scale. A simulation study evaluates the empirical performance of our proposed estimators under a wide range of scenarios. Finally, we discuss broader uses of test-negative outcomes to de-bias cohort studies in which testing is triggered by symptoms.
Authors
- Christopher Boyer (ORCID: https://orcid.org/0000-0002-1101-2045)
- Eric J. Tchetgen Tchetgen (ORCID: https://orcid.org/0000-0002-8369-3900)
- Kendrick Qijun Li (ORCID: https://orcid.org/0000-0003-3040-7250)
- Xu Shi (ORCID: https://orcid.org/0000-0001-8566-9552)
Institutions
- St. Jude Children's Research Hospital (US)
- Cleveland Clinic (US)
- University of Michigan (US)
- Cleveland Clinic Lerner College of Medicine (US)
- Case Western Reserve University (US)
- University of Pennsylvania (US)
Publication Details
- Journal
- Epidemiology
- Published
- 2025-11-25
- DOI
- https://doi.org/10.1097/ede.0000000000001926
- Primary Topic
- Advanced Causal Inference Techniques
- Type
- article
- Field-Weighted Citation Impact
- 0.00