Repositioning GLP-1 Receptor Agonists in Endometrial Cancer: Molecular Rationale, Preclinical Insights, and Translational Opportunities
Endometrial cancer incidence and mortality are rising globally, largely driven by the obesity epidemic. Treatment options remain limited for obesity-associated, hormone-resistant, or fertility-preserving endometrial cancer, highlighting the need for novel therapies that address both tumor biology and metabolic dysfunction. In this study, we synthesize the molecular rationale, preclinical, population-based, and emerging clinical trial evidence on glucagon-like peptide-1 receptor (GLP-1R) agonists (GLP-1 RA) in endometrial cancer. GLP-1R is expressed in benign and malignant endometrial tissues, where activation of cAMP-PKA and AMPK-mTOR signaling has been shown to mediate antiproliferative, proapoptotic, and autophagy-inducing effects. Preclinical models demonstrate that class-wide GLP-1 RAs may restore progesterone receptor expression, overcome hormone resistance, and synergize with progestin therapy; however, the effects may vary by agent. Retrospective studies suggest that combining GLP-1 RAs with local progestin therapy, commonly a levonorgestrel-releasing intrauterine device (preferred in obesity because oral progestin bioavailability is reduced), is associated with a reduced risk of endometrial cancer in high-risk women. Ongoing clinical trials are assessing their role in fertility-sparing settings-evaluating complete response to progestin-based therapy, relapse rates, and time to conception outcomes-as well as in adjuvant settings, in which disease-free survival is a key endpoint; however, gastrointestinal tolerability and the absence of long-term safety data in endometrial cancer populations remain important considerations. As a class, GLP-1 RAs represent a promising therapeutic approach to targeting both the obesogenic milieu and tumor-intrinsic pathways in endometrial cancer; however, agent-specific differences warrant attention. Prospective, subtype-stratified trials are essential to establish their role in comprehensive endometrial cancer care.
Authors
- Matthew A. Powell (ORCID: https://orcid.org/0000-0002-9001-3862)
- Robert Louis Coleman (ORCID: https://orcid.org/0000-0001-9343-8754)
- Vivek Podder (ORCID: https://orcid.org/0000-0003-3103-3043)
- Priya Singhania (ORCID: https://orcid.org/0009-0003-3707-955X)
- Andrea R. Hagemann (ORCID: https://orcid.org/0000-0002-3484-0046)
- Brian M. Slomovitz (ORCID: https://orcid.org/0000-0002-7241-3096)
- Thomas J. Herzog (ORCID: https://orcid.org/0000-0002-4584-8908)
Institutions
- Washington University in St. Louis (US)
- Texas Oncology (US)
- Bangladesh Islami University (BD)
- Mount Sinai Medical Center (US)
- The US Oncology Network (US)
- Shaheed Suhrawardy Medical College (BD)
- University of Cincinnati (US)
- University of Cincinnati Medical Center (US)
Publication Details
- Journal
- Clinical Cancer Research
- Published
- 2025-12-02
- DOI
- https://doi.org/10.1158/1078-0432.ccr-25-2819
- Primary Topic
- Diabetes Treatment and Management
- Type
- article
- Field-Weighted Citation Impact
- 0.00