Clinical Phenotype and Prognosis of Real-World Patients with Wild-Type Transthyretin Amyloid Cardiomyopathy Treated with Tafamidis

In this large, contemporary, real-world cohort of patients with ATTRwt-CM, predominantly in NYHA class I or II, treatment with tafamidis was consistently associated with a significantly lower risk of all-cause mortality.

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Publication Details

Journal
European Journal of Heart Failure
Published
2025-11-29
DOI
https://doi.org/10.1002/ejhf.70071
Citations
3
Primary Topic
Amyloidosis: Diagnosis, Treatment, Outcomes
Type
article
Field-Weighted Citation Impact
2.42

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article

Clinical Phenotype and Prognosis of Real-World Patients with Wild-Type Transthyretin Amyloid Cardiomyopathy Treated with Tafamidis

Matteo Serenelli, Stefano Perlini, Giuseppe D. Sanna, Alberto Cipriani et al.
3 citations
European Journal of Heart Failure
Amyloidosis: Diagnosis, Treatment, Outcomes
2.42
article

Clinical Phenotype and Prognosis of Real-World Patients with Wild-Type Transthyretin Amyloid Cardiomyopathy Treated with Tafamidis

Matteo Serenelli, Stefano Perlini, Giuseppe D. Sanna, Alberto Cipriani, Simone Longhi, Piero Gentile, Beatrice Musumeci, Giacomo Bonacchi, Fabio Vagnarelli, Paolo Milani, Emanuele Monda, Michele Emdin, Gianfranco Sinagra, Laura De Michieli, Gianluca Di Bella, Giuseppe Vergaro, Federico Perfetto, Carla Lofiego, Emilia D’Elia, Giuseppe Limongelli, Massimo Imazio, Marco Metra, Daniela Tomasoni, Marco Merlo, Samuela Carigi, Francesca Sturdà, Irene Ruotolo, Giulio Sinigiani, Mauro Driussi, Marco Marini, Elisa Gardini, Giacomo Tini, Guido De Sena, Aldostefano Porcari, Marco Canepa, Elena Biagini, Marco Pozzan, Francesco Cappelli, Michela Bartolotti, Giampaolo Merlini, Stefania Marazìa, Federica Colio, Grazia Foti, Giovanni Palladini, Margherita Zanoletti, Alberto Aimo, Francesco Musca, Anna Cantone, Massimo Di Marco
article en
3 citations

Abstract

In this large, contemporary, real-world cohort of patients with ATTRwt-CM, predominantly in NYHA class I or II, treatment with tafamidis was consistently associated with a significantly lower risk of all-cause mortality.

European Journal of Heart FailureVol. 27(12)
University of Messina (IT), University of Padua (IT), University of Trieste (IT), University of Sassari (IT), University of Ferrara (IT), University of Pavia (IT), The Royal Free Hospital (GB), Azienda Socio Sanitaria Territoriale Grande Ospedale Metropolitano Niguarda (IT), Surgical Specialties (Canada) (CA), Azienda Socio Sanitaria Territoriale degli Spedali Civili di Brescia (IT), Ospedale Papa Giovanni XXIII (IT), Ospedale di Santo Spirito (IT), Amyloidosis Foundation (US), Ospedale “M. Bufalini” di Cesena (IT), Azienda Ospedaliero-Universitaria Careggi (IT), Azienda USL di Bologna (IT), Ospedale G.B. Morgagni - L.Pierantoni (IT), Equilibrium Research (GB), Ospedale Santa Maria della Misericordia di Udine (IT), University of Campania "Luigi Vanvitelli" (IT), Ospedale Infermi di Rimini (IT), Ospedale Monaldi (IT), ERN GUARD-Heart (NL), European Hospital (IT), Ospedale Policlinico San Martino (IT), Policlinico San Matteo Fondazione (IT), Ospedale Vito Fazzi (IT), Istituti di Ricovero e Cura a Carattere Scientifico (IT), Fondazione Toscana Gabriele Monasterio (IT), Azienda Sanitaria Universitaria Integrata di Trieste (IT), Ospedali Riuniti Umberto I (IT), University of Florence (IT), University College London (GB), Misericordia University (US), University of Brescia (IT), University of Genoa (IT), Sapienza University of Rome (IT), University of Bologna (IT)
Bristol-Myers Squibb, Pfizer, AstraZeneca, Sanofi, Alexion Pharmaceuticals, Alnylam Pharmaceuticals, Boston Scientific Corporation, Regeneron Pharmaceuticals, Amicus Therapeutics, Prothena, Ministero della Salute, Novo Nordisk, Vifor Pharma, Sanofi Genzyme, Daiichi Sankyo Europe
Openalex Percentile: Top 10%
Amyloidosis: Diagnosis, Treatment, Outcomes
2.42
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