Clinical Phenotype and Prognosis of Real-World Patients with Wild-Type Transthyretin Amyloid Cardiomyopathy Treated with Tafamidis
In this large, contemporary, real-world cohort of patients with ATTRwt-CM, predominantly in NYHA class I or II, treatment with tafamidis was consistently associated with a significantly lower risk of all-cause mortality.
Authors
- Matteo Serenelli (ORCID: https://orcid.org/0000-0002-8947-7176)
- Stefano Perlini (ORCID: https://orcid.org/0000-0002-0320-8574)
- Giuseppe D. Sanna (ORCID: https://orcid.org/0000-0002-3357-0961)
- Alberto Cipriani (ORCID: https://orcid.org/0000-0001-7842-6202)
- Simone Longhi (ORCID: https://orcid.org/0000-0002-7512-1179)
- Piero Gentile (ORCID: https://orcid.org/0000-0003-3360-3548)
- Beatrice Musumeci (ORCID: https://orcid.org/0000-0003-4872-7981)
- Giacomo Bonacchi (ORCID: https://orcid.org/0000-0001-8305-5274)
- Fabio Vagnarelli (ORCID: https://orcid.org/0009-0006-0993-061X)
- Paolo Milani (ORCID: https://orcid.org/0000-0002-0409-6201)
- Emanuele Monda (ORCID: https://orcid.org/0000-0001-9304-988X)
- Michele Emdin (ORCID: https://orcid.org/0000-0002-8541-1962)
- Gianfranco Sinagra (ORCID: https://orcid.org/0000-0003-2700-8478)
- Laura De Michieli (ORCID: https://orcid.org/0000-0003-0574-4052)
- Gianluca Di Bella (ORCID: https://orcid.org/0000-0001-8933-9884)
- Giuseppe Vergaro (ORCID: https://orcid.org/0000-0002-7066-6006)
- Federico Perfetto (ORCID: https://orcid.org/0000-0003-0276-8331)
- Carla Lofiego
- Emilia D’Elia (ORCID: https://orcid.org/0000-0002-6682-0074)
- Giuseppe Limongelli (ORCID: https://orcid.org/0000-0002-8291-9517)
- Massimo Imazio (ORCID: https://orcid.org/0000-0002-5722-0245)
- Marco Metra (ORCID: https://orcid.org/0000-0001-6691-8568)
- Daniela Tomasoni (ORCID: https://orcid.org/0000-0002-7584-2857)
- Marco Merlo (ORCID: https://orcid.org/0000-0002-1022-3131)
- Samuela Carigi (ORCID: https://orcid.org/0000-0002-2429-1135)
- Francesca Sturdà (ORCID: https://orcid.org/0000-0003-3480-6806)
- Irene Ruotolo (ORCID: https://orcid.org/0009-0002-6120-0287)
- Giulio Sinigiani (ORCID: https://orcid.org/0000-0001-5736-6829)
- Mauro Driussi
- Marco Marini (ORCID: https://orcid.org/0000-0003-2165-556X)
- Elisa Gardini
- Giacomo Tini (ORCID: https://orcid.org/0000-0001-8520-152X)
- Guido De Sena (ORCID: https://orcid.org/0009-0009-6469-3786)
- Aldostefano Porcari (ORCID: https://orcid.org/0000-0003-3307-0825)
- Marco Canepa (ORCID: https://orcid.org/0000-0001-9063-5576)
- Elena Biagini (ORCID: https://orcid.org/0000-0003-0295-0440)
- Marco Pozzan (ORCID: https://orcid.org/0000-0001-7222-5231)
- Francesco Cappelli (ORCID: https://orcid.org/0000-0002-1622-0732)
- Michela Bartolotti
- Giampaolo Merlini (ORCID: https://orcid.org/0000-0001-7680-3254)
- Stefania Marazìa
- Federica Colio
- Grazia Foti
- Giovanni Palladini
- Margherita Zanoletti
- Alberto Aimo
- Francesco Musca
- Anna Cantone (ORCID: https://orcid.org/0000-0002-8125-5536)
- Massimo Di Marco (ORCID: https://orcid.org/0000-0002-4423-5202)
Institutions
- University of Messina (IT)
- University of Padua (IT)
- University of Trieste (IT)
- University of Sassari (IT)
- University of Ferrara (IT)
- University of Pavia (IT)
- The Royal Free Hospital (GB)
- Azienda Socio Sanitaria Territoriale Grande Ospedale Metropolitano Niguarda (IT)
- Surgical Specialties (Canada) (CA)
- Azienda Socio Sanitaria Territoriale degli Spedali Civili di Brescia (IT)
- Ospedale Papa Giovanni XXIII (IT)
- Ospedale di Santo Spirito (IT)
- Amyloidosis Foundation (US)
- Ospedale “M. Bufalini” di Cesena (IT)
- Azienda Ospedaliero-Universitaria Careggi (IT)
- Azienda USL di Bologna (IT)
- Ospedale G.B. Morgagni - L.Pierantoni (IT)
- Equilibrium Research (GB)
- Ospedale Santa Maria della Misericordia di Udine (IT)
- University of Campania "Luigi Vanvitelli" (IT)
- Ospedale Infermi di Rimini (IT)
- Ospedale Monaldi (IT)
- ERN GUARD-Heart (NL)
- European Hospital (IT)
- Ospedale Policlinico San Martino (IT)
- Policlinico San Matteo Fondazione (IT)
- Ospedale Vito Fazzi (IT)
- Istituti di Ricovero e Cura a Carattere Scientifico (IT)
- Fondazione Toscana Gabriele Monasterio (IT)
- Azienda Sanitaria Universitaria Integrata di Trieste (IT)
- Ospedali Riuniti Umberto I (IT)
- University of Florence (IT)
- University College London (GB)
- Misericordia University (US)
- University of Brescia (IT)
- University of Genoa (IT)
- Sapienza University of Rome (IT)
- University of Bologna (IT)
Publication Details
- Journal
- European Journal of Heart Failure
- Published
- 2025-11-29
- DOI
- https://doi.org/10.1002/ejhf.70071
- Citations
- 3
- Primary Topic
- Amyloidosis: Diagnosis, Treatment, Outcomes
- Type
- article
- Field-Weighted Citation Impact
- 2.42
Funders
- Bristol-Myers Squibb
- Pfizer
- AstraZeneca
- Sanofi
- Alexion Pharmaceuticals
- Alnylam Pharmaceuticals
- Boston Scientific Corporation
- Regeneron Pharmaceuticals
- Amicus Therapeutics
- Prothena
- Ministero della Salute
- Novo Nordisk
- Vifor Pharma
- Sanofi Genzyme
- Daiichi Sankyo Europe