Qualitative Research in Children and Parents of Children with Achondroplasia to Evaluate the Content Validity of Multiple Clinical Outcome Assessments
The PedsQL, QoLISSY, Pain-NRS, and WeeFIM are content valid, appropriate, and relevant to include in future studies of individuals with achondroplasia.
Authors
- Ravi Savarirayan (ORCID: https://orcid.org/0000-0002-5105-8427)
- Daniela Rogoff
- Elena Muslimova
- Hilary H. Colwell
- Julie Hoover‐Fong (ORCID: https://orcid.org/0000-0002-1242-5626)
- Chandler Crews
- Susana Noval Iruretagoyena
- Susan D. Mathias (ORCID: https://orcid.org/0000-0002-2812-7033)
- Inês Alves (ORCID: https://orcid.org/0000-0002-3914-7101)
- Amer Haider
- Anne Grumet
Institutions
- Johns Hopkins University (US)
- WuFeng University (TW)
- University of Évora (PT)
- Johns Hopkins Medicine (US)
- Health Outcomes Solutions (United States) (US)
- Fundación Hospital de Jove (ES)
- Université Bourgogne Franche-Comté (FR)
- Murdoch Children's Research Institute (AU)
- Nemours Children's Clinic (US)
- Bridge Pharma (United States) (US)
- Arkansas Department of Agriculture (US)
Publication Details
- Journal
- Advances in Therapy
- Published
- 2025-11-28
- DOI
- https://doi.org/10.1007/s12325-025-03425-y
- Primary Topic
- Connective tissue disorders research
- Type
- article
- Field-Weighted Citation Impact
- 0.00