Advances in cystic fibrosis: CFTR modulator triple combinations
<title>Shareable abstract</title> Triple combinations of CFTR modulators have revolutionized the care of people with cystic fibrosis (CF). Initially developed for the F508del variant, these drugs are effective in many other <italic>CFTR</italic> variants, making them suitable for most, but not all, pwCF.
Authors
- Marcus Alexander Mall (ORCID: https://orcid.org/0000-0002-4057-2199)
- Pierre‐Régis Burgel (ORCID: https://orcid.org/0000-0003-0903-9828)
Institutions
- Goethe University Frankfurt (DE)
- Inserm (FR)
- Université Paris Cité (FR)
- Hôpital Cochin (FR)
- Assistance Publique – Hôpitaux de Paris (FR)
- Cardiovascular Center Frankfurt (DE)
- German Center for Lung Research (DE)
- Institut Cochin (FR)
- Charité - Universitätsmedizin Berlin (DE)
Publication Details
- Journal
- European Respiratory Journal
- Published
- 2025-11-27
- DOI
- https://doi.org/10.1183/13993003.01783-2025
- Citations
- 3
- Primary Topic
- Cystic Fibrosis Research Advances
- Type
- article
- Field-Weighted Citation Impact
- 4.56