Advances in cystic fibrosis: CFTR modulator triple combinations

<title>Shareable abstract</title> Triple combinations of CFTR modulators have revolutionized the care of people with cystic fibrosis (CF). Initially developed for the F508del variant, these drugs are effective in many other <italic>CFTR</italic> variants, making them suitable for most, but not all, pwCF.

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Publication Details

Journal
European Respiratory Journal
Published
2025-11-27
DOI
https://doi.org/10.1183/13993003.01783-2025
Citations
3
Primary Topic
Cystic Fibrosis Research Advances
Type
article
Field-Weighted Citation Impact
4.56
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article

Advances in cystic fibrosis: CFTR modulator triple combinations

Marcus Alexander Mall, Pierre‐Régis Burgel
3 citations
European Respiratory Journal
Cystic Fibrosis Research Advances
4.56
article

Advances in cystic fibrosis: CFTR modulator triple combinations

Marcus Alexander Mall, Pierre‐Régis Burgel
article en
3 citations

Abstract

<title>Shareable abstract</title> Triple combinations of CFTR modulators have revolutionized the care of people with cystic fibrosis (CF). Initially developed for the F508del variant, these drugs are effective in many other <italic>CFTR</italic> variants, making them suitable for most, but not all, pwCF.

European Respiratory JournalVol. 67(1)
Goethe University Frankfurt (DE), Inserm (FR), Université Paris Cité (FR), Hôpital Cochin (FR), Assistance Publique – Hôpitaux de Paris (FR), Cardiovascular Center Frankfurt (DE), German Center for Lung Research (DE), Institut Cochin (FR), Charité - Universitätsmedizin Berlin (DE)
Openalex Percentile: Top 5%
Cystic Fibrosis Research Advances
4.56
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Advances in cystic fibrosis: CFTR modulator triple combinations — Marcus Alexander Mall, Pierre‐Régis Burgel · European Respiratory Journal (2025) | TGRS Research Map | TGRS