Cellular immune endophenotypes separating early and late-onset myasthenia gravis
The 2 main subgroups of autoimmune myasthenia gravis, a neuromuscular junction disorder associated with muscle weakness, are early- and late-onset forms, defined by onset before or after 50 years of age. Both carry acetylcholine-receptor autoantibodies but differ in sex ratios, genetics, and occurrence of disease-specific thymus inflammation. To distinguish the 2 forms by cellular immune phenotyping, we applied multimodal techniques, including deep spectral cytometric phenotyping and single-cell sequencing. Analysis of 2 independent cohorts identified immunological differences driven by 3 main lymphocyte populations. Lower frequencies of mucosa-associated invariant T cells and naive CD8+ T cells were observed in late-onset myasthenia, suggesting enhanced immune senescence. A highly differentiated, canonical NK cell population was reduced in early-onset myasthenia and negatively correlated with the degree of thymic hyperplasia. Using only the frequency of these 3 populations, correct myasthenia subgroup assignment could be predicted with 90% accuracy. These distinct immunocellular endophenotypes for early- and late-onset disease suggest differences in immunopathogenic processes. Along with demographic factors and other disease subgroup-specific features, the frequency of the identified cell subpopulations may improve clinical classification.
Authors
- Nicolas Ruffin (ORCID: https://orcid.org/0000-0002-3698-5505)
- Jakob Theorell (ORCID: https://orcid.org/0000-0001-8752-3151)
- Chiara Sorini (ORCID: https://orcid.org/0000-0002-6803-8377)
- Adam E. Handel (ORCID: https://orcid.org/0000-0001-8385-6346)
- Sarosh R. Irani (ORCID: https://orcid.org/0000-0002-7667-9748)
- Valentina Damato (ORCID: https://orcid.org/0000-0003-1740-4522)
- Andrew Fower (ORCID: https://orcid.org/0000-0003-0414-2367)
- Susanna Brauner (ORCID: https://orcid.org/0000-0002-9120-9488)
- Lahiru Handunnetthi (ORCID: https://orcid.org/0000-0002-8242-3722)
- Philip Ambrose
- Fredrik Piehl (ORCID: https://orcid.org/0000-0001-8329-5219)
- Isabel Leite
Institutions
- Karolinska University Hospital (SE)
- Centre for Human Genetics (GB)
- Jacksonville College (US)
- Karolinska Institutet (SE)
- University of Oxford (GB)
- Centre For Human Genetics (IN)
- Science Oxford (GB)
- Mayo Clinic in Florida (US)
- University of Florence (IT)
Publication Details
- Journal
- JCI Insight
- Published
- 2025-11-27
- DOI
- https://doi.org/10.1172/jci.insight.199679
- Primary Topic
- Myasthenia Gravis and Thymoma
- Type
- article
- Field-Weighted Citation Impact
- 0.00
Funders
- Wellcome Trust
- National Institute for Health and Care Research
- University of Oxford
- Knut och Alice Wallenbergs Stiftelse
- Vetenskapsrådet
- Science for Life Laboratory
- Medical Research Council
- Uppsala Multidisciplinary Center for Advanced Computational Science