Condition-Specific Growth Charts for Children With Alagille Syndrome
These findings suggest that condition-specific growth charts for ALGS may provide a crucial tool for clinicians to evaluate growth and aid in decision-making around listing children for liver transplant.
Authors
- Giuseppe Indolfi (ORCID: https://orcid.org/0000-0003-3830-9823)
- Nehal M. El-Koofy (ORCID: https://orcid.org/0000-0002-7464-6715)
- Björn Fischler (ORCID: https://orcid.org/0000-0002-8838-324X)
- Chatmanee Lertudomphonwanit (ORCID: https://orcid.org/0000-0001-6838-2656)
- John Eshun (ORCID: https://orcid.org/0000-0001-8285-9123)
- Déirdre Kelly (ORCID: https://orcid.org/0000-0001-9776-4354)
- Christina Hajinicolaou
- M. Kyle Jensen
- Shannon M. Vandriel (ORCID: https://orcid.org/0000-0001-7157-2063)
- Emmanuel M. Gonzales (ORCID: https://orcid.org/0000-0002-1546-3193)
- Saul J. Karpen (ORCID: https://orcid.org/0000-0002-3379-7592)
- Tanguy Demaret (ORCID: https://orcid.org/0000-0001-7605-9031)
- Jane Hartley (ORCID: https://orcid.org/0000-0002-4201-6460)
- Jesús Quintero (ORCID: https://orcid.org/0000-0002-6456-9031)
- Seema Alam (ORCID: https://orcid.org/0000-0003-0888-8625)
- Catalina Jaramillo (ORCID: https://orcid.org/0000-0003-0437-6569)
- Mathieu Roelants (ORCID: https://orcid.org/0000-0002-3749-0475)
- Henrik Arnell (ORCID: https://orcid.org/0000-0001-5012-8203)
- Jeffrey A. Feinstein (ORCID: https://orcid.org/0000-0002-6078-5976)
- Pınar Bulut (ORCID: https://orcid.org/0000-0003-0709-855X)
- Pamela L. Valentino (ORCID: https://orcid.org/0000-0002-8227-2004)
- Cristina Gonçalves (ORCID: https://orcid.org/0000-0003-2755-3513)
- Sabina Więcek (ORCID: https://orcid.org/0000-0001-9870-6674)
- Bettina E. Hansen (ORCID: https://orcid.org/0000-0001-8307-3341)
- Henkjan J. Verkade (ORCID: https://orcid.org/0000-0002-7034-2861)
- Elisa de Carvalho (ORCID: https://orcid.org/0000-0002-5079-5011)
- Quais Mujawar (ORCID: https://orcid.org/0000-0002-0181-5434)
- Amin J. Roberts (ORCID: https://orcid.org/0000-0001-7873-7385)
- Rubén E. Quirós‐Tejeira (ORCID: https://orcid.org/0009-0000-1163-5202)
- Winita Hardikar (ORCID: https://orcid.org/0000-0003-4277-2773)
- Étienne Sokal (ORCID: https://orcid.org/0000-0001-5597-4708)
- Mureo Kasahara (ORCID: https://orcid.org/0000-0002-1651-0430)
- Emanuele Nicastro (ORCID: https://orcid.org/0000-0002-4518-9375)
- Zerrin Önal (ORCID: https://orcid.org/0000-0002-7627-7423)
- Sahana Shankar (ORCID: https://orcid.org/0000-0002-8162-2324)
- Dorota Gliwicz‐Miedzińska
- Henry C. Lin (ORCID: https://orcid.org/0000-0002-1263-5404)
- Noelle H. Ebel (ORCID: https://orcid.org/0000-0003-4494-1729)
- Ryan T. Fischer (ORCID: https://orcid.org/0000-0002-2576-4694)
- Nathalie Rock (ORCID: https://orcid.org/0000-0001-5315-9267)
- Kathleen B. Schwarz (ORCID: https://orcid.org/0000-0003-0753-0402)
- Jérôme Bouligand (ORCID: https://orcid.org/0000-0002-8691-9469)
- Çiğdem Arıkan (ORCID: https://orcid.org/0000-0002-0794-2741)
- Melina Melere (ORCID: https://orcid.org/0000-0003-2611-3161)
- Lorenzo D’Antiga (ORCID: https://orcid.org/0000-0001-7150-3148)
- Jian‐She Wang (ORCID: https://orcid.org/0000-0003-0823-586X)
- Helen Evans (ORCID: https://orcid.org/0000-0002-8860-2705)
- Pier Luigi Calvo (ORCID: https://orcid.org/0000-0001-9264-3465)
- Dominique Debray (ORCID: https://orcid.org/0000-0002-0345-963X)
- Niviann Blondet (ORCID: https://orcid.org/0000-0001-5122-0706)
- Maria Lorena Cavalieri
- Wikrom W. Karnsakul (ORCID: https://orcid.org/0000-0001-7288-5459)
- Shikha S. Sundaram (ORCID: https://orcid.org/0000-0003-2523-6389)
- James E. Squires (ORCID: https://orcid.org/0000-0001-6979-8987)
- Kathleen M. Loomes (ORCID: https://orcid.org/0000-0002-1539-6672)
- Silvia Nastasio (ORCID: https://orcid.org/0000-0003-0200-5326)
- Piotr Czubkowski (ORCID: https://orcid.org/0000-0002-0332-5703)
- Jernej Brecelj (ORCID: https://orcid.org/0000-0002-7871-8325)
- Binita M. Kamath (ORCID: https://orcid.org/0009-0002-2023-304X)
- Aglaia Zellos
- Catherine M. Larson‐Nath (ORCID: https://orcid.org/0000-0001-8797-2651)
- Ermelinda Santos Silva (ORCID: https://orcid.org/0000-0002-0987-341X)
- René Romero (ORCID: https://orcid.org/0000-0002-1566-2280)
- Koen Huysentruyt (ORCID: https://orcid.org/0000-0002-6402-1762)
- Maria E. Rogalidou (ORCID: https://orcid.org/0000-0001-5617-2432)
- Raquel Borges Pinto (ORCID: https://orcid.org/0000-0002-5521-7528)
- Andréanne N. Zizzo (ORCID: https://orcid.org/0000-0001-6350-2057)
- Antal Dezsőfi‐Gottl (ORCID: https://orcid.org/0000-0001-7170-3959)
- Irena Jankowska (ORCID: https://orcid.org/0000-0001-6847-9570)
- Emmanuel Jacquemin (ORCID: https://orcid.org/0000-0002-7536-6272)
- Seak Hee Oh (ORCID: https://orcid.org/0000-0002-9672-8877)
- Carolina Jiménez‐Rivera (ORCID: https://orcid.org/0000-0002-1330-1043)
- Christos Tzivinikos (ORCID: https://orcid.org/0000-0001-9681-1649)
- María Legarda Tamara
- Michael Stormon (ORCID: https://orcid.org/0000-0002-3614-7085)
- Nanda Kerkar (ORCID: https://orcid.org/0000-0003-0978-1491)
- Gabriella Nebbia (ORCID: https://orcid.org/0000-0003-1810-7722)
- Luís Bujanda (ORCID: https://orcid.org/0000-0002-4353-9968)
- Way Seah Lee (ORCID: https://orcid.org/0000-0001-9163-2828)
- Cristina Molera Busoms (ORCID: https://orcid.org/0000-0002-1193-6803)
- Florence Lacaille
- Amal Aqul
- Elizabeth B. Rand (ORCID: https://orcid.org/0000-0002-1173-4558)
- Mohamed A. Elmonem (ORCID: https://orcid.org/0000-0002-3154-1948)
- Kyung Mo Kim (ORCID: https://orcid.org/0000-0001-7896-6751)
- Tim Cole (ORCID: https://orcid.org/0000-0001-5711-8200)
- Jennifer García (ORCID: https://orcid.org/0000-0001-7557-3063)
- Richard J. Thompson
- Liting Li
- Yael Mozer‐Glassberg (ORCID: https://orcid.org/0000-0003-2577-6860)
- Rima Fawaz (ORCID: https://orcid.org/0009-0005-2598-3319)
- David A. Piccoli
- Maria Camila Sanchez
- Victorien M. Wolters
- Marisa Renata Beretta (ORCID: https://orcid.org/0009-0007-3048-1027)
- Susan Siew (ORCID: https://orcid.org/0000-0002-8987-119X)
Institutions
- Semmelweis University (HU)
- University of Geneva (CH)
- Ulsan College (KR)
- Hebron University (PS)
- Western University (CA)
- Hôpital Necker-Enfants Malades (FR)
- Boston Children's Hospital (US)
- University of Minnesota (US)
- Hospital Sant Joan de Déu Barcelona (ES)
- Cliniques Universitaires Saint-Luc (BE)
- European Union (BE)
- Royal Children's Hospital (AU)
- Primary Children's Hospital (US)
- University Health Network (CA)
- Children's Mercy Hospital (US)
- Lucile Packard Children's Hospital (US)
- University Medical Center Groningen (NL)
- Karolinska University Hospital (SE)
- Children's Hospital of Philadelphia (US)
- Universidade Federal de Ciências da Saúde de Porto Alegre (BR)
- Vrije Universiteit Brussel (BE)
- Koç University (TR)
- Johns Hopkins University (US)
- Cairo University (EG)
- Inserm (FR)
- Oregon Health & Science University (US)
- Medical University of Silesia (PL)
- University of Groningen (NL)
- University of Pittsburgh (US)
- Palo Alto University (US)
- Universidade do Porto (PT)
- King's College London (GB)
- Virginia Commonwealth University (US)
- University of Toronto (CA)
- University of the Witwatersrand (ZA)
- Mahidol University (TH)
- Université Paris-Saclay (FR)
- Children's Hospital of Eastern Ontario (CA)
- Johns Hopkins Medicine (US)
- Chris Hani Baragwanath Hospital (ZA)
- Great Ormond Street Hospital (GB)
- Santa Casa Hospital (BR)
- Hospital Universitario La Paz (ES)
- London Health Sciences Centre (CA)
- Hospital for Sick Children (CA)
- Ljubljana University Medical Centre (SI)
- Asan Medical Center (KR)
- Toronto General Hospital (CA)
- Hospital Italiano de Buenos Aires (AR)
- Children's Hospital at Westmead (AU)
- Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico (IT)
- University of Rochester Medical Center (US)
- Narayana Health (IN)
- University Medical Center Utrecht (NL)
- Yale University (US)
- University of Malaya (MY)
- University of Ulsan (KR)
- Institut Necker Enfants Malades (FR)
- Azienda Ospedaliera Citta' della Salute e della Scienza di Torino (IT)
- Rady Children's Hospital-San Diego (US)
- Massachusetts General Hospital (US)
- Institute of Health Services and Policy Research (CA)
- Children's Hospital Colorado (US)
- Assistance Publique – Hôpitaux de Paris (FR)
- Birmingham Women's Hospital (GB)
- Biogipuzkoa Health Research Institute (ES)
- Birmingham Children's Hospital (GB)
- Ospedale Papa Giovanni XXIII (IT)
- Mohammed Bin Rashid University of Medicine and Health Sciences (AE)
- Seattle Children's Hospital (US)
- Schneider Children's Medical Center (IL)
- Azienda Ospedaliera San Gerardo (IT)
- Meyer Children's Hospital (IT)
- Children's Memorial Health Institute (PL)
- Wits University Donald Gordon Medical Centre (ZA)
- Institute of Liver and Biliary Sciences (IN)
- Phoenix Children's Hospital (US)
- Vall d'Hebron Hospital Universitari (ES)
- Grupo Hospitalar Conceição (BR)
- Mitera Hospital (GR)
- National Center For Child Health and Development (JP)
- University of Minnesota Medical Center (US)
- Hospital Universitário de Brasília (BR)
- Stanford Medicine (US)
- Hospital de Cruces (ES)
- Ramathibodi Hospital (TH)
- Starship Children's Health (NZ)
- Children's Healthcare of Atlanta (US)
- Children's Hospital of Western Ontario (CA)
- Children's Hospital & Medical Center (US)
- Miami Transplant Institute (US)
- Centro Hospitalar do Porto (PT)
- Birmingham Women’s and Children’s NHS Foundation Trust (GB)
- Le Bonheur Children's Hospital (US)
- Children's Hospital of Fudan University (CN)
- Iaso Children’s Hospital (GR)
- Bicêtre Hospital (FR)
- University College London (GB)
- University of Manitoba (CA)
- University of Nebraska Medical Center (US)
- University of Milano-Bicocca (IT)
- Istanbul University (TR)
- University of Silesia in Katowice (PL)
- The University of Texas Southwestern Medical Center (US)
- University of Colorado Denver (US)
- Stanford University (US)
- KU Leuven (BE)
Publication Details
- Journal
- JAMA Network Open
- Published
- 2025-11-24
- DOI
- https://doi.org/10.1001/jamanetworkopen.2025.45294
- Citations
- 1
- Primary Topic
- Pediatric Hepatobiliary Diseases and Treatments
- Type
- article
- Field-Weighted Citation Impact
- 2.01
Funders
- Gilead Sciences
- Alnylam Pharmaceuticals
- CSL Behring
- Sarepta Therapeutics
- National Natural Science Foundation of China
- Fudan University
- Hospital for Sick Children
- Ipsen
- Grifols
- National Institute of Diabetes and Digestive and Kidney Diseases