Condition-Specific Growth Charts for Children With Alagille Syndrome

These findings suggest that condition-specific growth charts for ALGS may provide a crucial tool for clinicians to evaluate growth and aid in decision-making around listing children for liver transplant.

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Publication Details

Journal
JAMA Network Open
Published
2025-11-24
DOI
https://doi.org/10.1001/jamanetworkopen.2025.45294
Citations
1
Primary Topic
Pediatric Hepatobiliary Diseases and Treatments
Type
article
Field-Weighted Citation Impact
2.01

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article

Condition-Specific Growth Charts for Children With Alagille Syndrome

Giuseppe Indolfi, Nehal M. El-Koofy, Björn Fischler, Chatmanee Lertudomphonwanit et al.
1 citations
JAMA Network Open
Pediatric Hepatobiliary Diseases and Treatments
2.01
article

Condition-Specific Growth Charts for Children With Alagille Syndrome

Giuseppe Indolfi, Nehal M. El-Koofy, Björn Fischler, Chatmanee Lertudomphonwanit, John Eshun, Déirdre Kelly, Christina Hajinicolaou, M. Kyle Jensen, Shannon M. Vandriel, Emmanuel M. Gonzales, Saul J. Karpen, Tanguy Demaret, Jane Hartley, Jesús Quintero, Seema Alam, Catalina Jaramillo, Mathieu Roelants, Henrik Arnell, Jeffrey A. Feinstein, Pınar Bulut, Pamela L. Valentino, Cristina Gonçalves, Sabina Więcek, Bettina E. Hansen, Henkjan J. Verkade, Elisa de Carvalho, Quais Mujawar, Amin J. Roberts, Rubén E. Quirós‐Tejeira, Winita Hardikar, Étienne Sokal, Mureo Kasahara, Emanuele Nicastro, Zerrin Önal, Sahana Shankar, Dorota Gliwicz‐Miedzińska, Henry C. Lin, Noelle H. Ebel, Ryan T. Fischer, Nathalie Rock, Kathleen B. Schwarz, Jérôme Bouligand, Çiğdem Arıkan, Melina Melere, Lorenzo D’Antiga, Jian‐She Wang, Helen Evans, Pier Luigi Calvo, Dominique Debray, Niviann Blondet, Maria Lorena Cavalieri, Wikrom W. Karnsakul, Shikha S. Sundaram, James E. Squires, Kathleen M. Loomes, Silvia Nastasio, Piotr Czubkowski, Jernej Brecelj, Binita M. Kamath, Aglaia Zellos, Catherine M. Larson‐Nath, Ermelinda Santos Silva, René Romero, Koen Huysentruyt, Maria E. Rogalidou, Raquel Borges Pinto, Andréanne N. Zizzo, Antal Dezsőfi‐Gottl, Irena Jankowska, Emmanuel Jacquemin, Seak Hee Oh, Carolina Jiménez‐Rivera, Christos Tzivinikos, María Legarda Tamara, Michael Stormon, Nanda Kerkar, Gabriella Nebbia, Luís Bujanda, Way Seah Lee, Cristina Molera Busoms, Florence Lacaille, Amal Aqul, Elizabeth B. Rand, Mohamed A. Elmonem, Kyung Mo Kim, Tim Cole, Jennifer García, Richard J. Thompson, Liting Li, Yael Mozer‐Glassberg, Rima Fawaz, David A. Piccoli, Maria Camila Sanchez, Victorien M. Wolters, Marisa Renata Beretta, Susan Siew
article en
1 citations

Abstract

These findings suggest that condition-specific growth charts for ALGS may provide a crucial tool for clinicians to evaluate growth and aid in decision-making around listing children for liver transplant.

JAMA Network OpenVol. 8(11)
Semmelweis University (HU), University of Geneva (CH), Ulsan College (KR), Hebron University (PS), Western University (CA), Hôpital Necker-Enfants Malades (FR), Boston Children's Hospital (US), University of Minnesota (US), Hospital Sant Joan de Déu Barcelona (ES), Cliniques Universitaires Saint-Luc (BE), European Union (BE), Royal Children's Hospital (AU), Primary Children's Hospital (US), University Health Network (CA), Children's Mercy Hospital (US), Lucile Packard Children's Hospital (US), University Medical Center Groningen (NL), Karolinska University Hospital (SE), Children's Hospital of Philadelphia (US), Universidade Federal de Ciências da Saúde de Porto Alegre (BR), Vrije Universiteit Brussel (BE), Koç University (TR), Johns Hopkins University (US), Cairo University (EG), Inserm (FR), Oregon Health & Science University (US), Medical University of Silesia (PL), University of Groningen (NL), University of Pittsburgh (US), Palo Alto University (US), Universidade do Porto (PT), King's College London (GB), Virginia Commonwealth University (US), University of Toronto (CA), University of the Witwatersrand (ZA), Mahidol University (TH), Université Paris-Saclay (FR), Children's Hospital of Eastern Ontario (CA), Johns Hopkins Medicine (US), Chris Hani Baragwanath Hospital (ZA), Great Ormond Street Hospital (GB), Santa Casa Hospital (BR), Hospital Universitario La Paz (ES), London Health Sciences Centre (CA), Hospital for Sick Children (CA), Ljubljana University Medical Centre (SI), Asan Medical Center (KR), Toronto General Hospital (CA), Hospital Italiano de Buenos Aires (AR), Children's Hospital at Westmead (AU), Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico (IT), University of Rochester Medical Center (US), Narayana Health (IN), University Medical Center Utrecht (NL), Yale University (US), University of Malaya (MY), University of Ulsan (KR), Institut Necker Enfants Malades (FR), Azienda Ospedaliera Citta' della Salute e della Scienza di Torino (IT), Rady Children's Hospital-San Diego (US), Massachusetts General Hospital (US), Institute of Health Services and Policy Research (CA), Children's Hospital Colorado (US), Assistance Publique – Hôpitaux de Paris (FR), Birmingham Women's Hospital (GB), Biogipuzkoa Health Research Institute (ES), Birmingham Children's Hospital (GB), Ospedale Papa Giovanni XXIII (IT), Mohammed Bin Rashid University of Medicine and Health Sciences (AE), Seattle Children's Hospital (US), Schneider Children's Medical Center (IL), Azienda Ospedaliera San Gerardo (IT), Meyer Children's Hospital (IT), Children's Memorial Health Institute (PL), Wits University Donald Gordon Medical Centre (ZA), Institute of Liver and Biliary Sciences (IN), Phoenix Children's Hospital (US), Vall d'Hebron Hospital Universitari (ES), Grupo Hospitalar Conceição (BR), Mitera Hospital (GR), National Center For Child Health and Development (JP), University of Minnesota Medical Center (US), Hospital Universitário de Brasília (BR), Stanford Medicine (US), Hospital de Cruces (ES), Ramathibodi Hospital (TH), Starship Children's Health (NZ), Children's Healthcare of Atlanta (US), Children's Hospital of Western Ontario (CA), Children's Hospital & Medical Center (US), Miami Transplant Institute (US), Centro Hospitalar do Porto (PT), Birmingham Women’s and Children’s NHS Foundation Trust (GB), Le Bonheur Children's Hospital (US), Children's Hospital of Fudan University (CN), Iaso Children’s Hospital (GR), Bicêtre Hospital (FR), University College London (GB), University of Manitoba (CA), University of Nebraska Medical Center (US), University of Milano-Bicocca (IT), Istanbul University (TR), University of Silesia in Katowice (PL), The University of Texas Southwestern Medical Center (US), University of Colorado Denver (US), Stanford University (US), KU Leuven (BE)
Gilead Sciences, Alnylam Pharmaceuticals, CSL Behring, Sarepta Therapeutics, National Natural Science Foundation of China, Fudan University, Hospital for Sick Children, Ipsen, Grifols, National Institute of Diabetes and Digestive and Kidney Diseases
Openalex Percentile: Top 10%
Pediatric Hepatobiliary Diseases and Treatments
2.01
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