Rational design and applications of piperazine and cyclohexane ionizable lipids for PKU and SSADH deficiency
Young Kee Shin, Diana D. Kang, Jeewon Kim, J. Bán et al.
Journal
Molecular Therapy — Nucleic Acids
Topics
Metabolism and Genetic Disorders
article
Rational design and applications of piperazine and cyclohexane ionizable lipids for PKU and SSADH deficiency
Young Kee Shin, Diana D. Kang, Jeewon Kim, J. Bán, Hyelim Park, Du Shi, Na Rae Lee, Yuebao Zhang, Seung‐Eun Chong, Shuishan Song, Hyeong‐Ahn Kwon, Jaesung Jung, Jungeun Lee, Eunyoung Park, Hyun‐Jung Yoo, Joonyoung Park, Eunhye Oh, Sang Jae Bae, Sun-Hee Kang, Yizhou Dong, Jae Uk Jeong, Jong-Keun Son