Caregiver-reported Patient Experiences with Duchenne Muscular Dystrophy: Qualitative In-trial Interviews 1 Year After Delandistrogene Moxeparvovec in the Pivotal EMBARK Trial

Authors

Teofil Ciobanu
Ivana Audhya
Christina Slota (ORCID: https://orcid.org/0000-0001-7509-3350)
Katherine Gooch (ORCID: https://orcid.org/0009-0000-6382-614X)
Susan Martin (ORCID: https://orcid.org/0000-0002-9594-5036)
A. Nascimento (ORCID: https://orcid.org/0000-0003-4952-5732)
Aravindhan Veerapandiyan (ORCID: https://orcid.org/0000-0002-3065-3956)
Buddha Basnyat (ORCID: https://orcid.org/0000-0002-1125-2743)
A. St. J. Murphy (ORCID: https://orcid.org/0000-0001-8337-4427)
Claire J. Lansdall
Alise B. Nacson

Institutions

Roche (Switzerland) (CH)
Arkansas Children's Hospital (US)
Hospital Sant Joan de Déu Barcelona (ES)
Hertfordshire Community NHS Trust (GB)
Roche (United Kingdom) (GB)
RTI Health Solutions (US)
Sant Joan de Déu Research Foundation (ES)
Sarepta Therapeutics (United States) (US)
University of Arkansas for Medical Sciences (US)

Publication Details

Journal: Neurology and Therapy
Published: 2025-11-03
DOI: https://doi.org/10.1007/s40120-025-00842-7
Primary Topic: Muscle Physiology and Disorders
Type: article
Field-Weighted Citation Impact: 0.00

Funders

Sarepta Therapeutics

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article

Caregiver-reported Patient Experiences with Duchenne Muscular Dystrophy: Qualitative In-trial Interviews 1 Year After Delandistrogene Moxeparvovec in the Pivotal EMBARK Trial

Teofil Ciobanu, Ivana Audhya, Christina Slota, Katherine Gooch et al.

Nov 3, 2025

Neurology and Therapy

Muscle Physiology and Disorders

article

Caregiver-reported Patient Experiences with Duchenne Muscular Dystrophy: Qualitative In-trial Interviews 1 Year After Delandistrogene Moxeparvovec in the Pivotal EMBARK Trial

Teofil Ciobanu, Ivana Audhya, Christina Slota, Katherine Gooch, Susan Martin, A. Nascimento, Aravindhan Veerapandiyan, Buddha Basnyat, A. St. J. Murphy, Claire J. Lansdall, Alise B. Nacson

November 3, 2025article en

Abstract

No abstract available for this paper.

Neurology and TherapyVol. 15(1)

Roche (Switzerland) (CH), Arkansas Children's Hospital (US), Hospital Sant Joan de Déu Barcelona (ES), Hertfordshire Community NHS Trust (GB), Roche (United Kingdom) (GB), RTI Health Solutions (US), Sant Joan de Déu Research Foundation (ES), Sarepta Therapeutics (United States) (US), University of Arkansas for Medical Sciences (US)

Sarepta Therapeutics

Openalex Percentile: Top 71%

Muscle Physiology and Disorders

DOI Open Access PDF OpenAlex

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Caregiver-reported Patient Experiences with Duchenne Muscular Dystrophy: Qualitative In-trial Interviews 1 Year After Delandistrogene Moxeparvovec in the Pivotal EMBARK Trial — Teofil Ciobanu, Ivana Audhya, et al. · Neurology and Therapy (2025) | TGRS Research Map | TGRS