Beyond Trikafta: new models to assess tissue dependent rescue of N1303K-CFTR

N1303K-CFTR shows tissue specific correction and suboptimal response to ETI which can be improved by API.

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Publication Details

Journal
Frontiers in Pharmacology
Published
2025-10-29
DOI
https://doi.org/10.3389/fphar.2025.1661417
Primary Topic
Atrial Fibrillation Management and Outcomes
Type
article
Field-Weighted Citation Impact
0.00

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article

Beyond Trikafta: new models to assess tissue dependent rescue of N1303K-CFTR

Renata Bocciardi, N. Caporelli, Camille Audousset, Sophie Ramel et al.
Frontiers in Pharmacology
Atrial Fibrillation Management and Outcomes
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Beyond Trikafta: new models to assess tissue dependent rescue of N1303K-CFTR

Renata Bocciardi, N. Caporelli, Camille Audousset, Sophie Ramel, Melissa Baravalle, Stefano Costa, Mairead Kelly, I. Durieu, M. Ensinck, Mirosław Zając, Alexandre Hinzpeter, Isabelle Sermet‐Gaudelus, Marianne Sylvia Carlon, Piercarlo Poli, Emanuela Pesce, Laure Cosson, Philippe Reix, S. Bui, M. Bulcaen, Julie Macey, B. Chevalier, Benoît Douvry, Federico Cresta, Aurélie Tatopoulos, Marco Cipolli, Cristina Pastorino, F. Chedevergne, Valeria Daccò, Vito Terlizzi, Aurélie Hatton, Cristina Lucanto, Jennifer Da Silva, Sonia Volpi, Laurence Le Clainche-Viala, Nicoletta Pedemonte, Laura Claut, Federico Zara, Marie Mittaine, Elise Dréano, Luis J. V. Galietta, Bénédicte Richaud-Thiriez, Bruno Ravoninjatovo, Emmanuelle Girodon, Guillaume Thouvenin, Iwona Pranke, Clémence Martin, Stefano Pantano, Mariateresa Lena, Valeria Tomati, Dominique Grenet, Pierre‐Régis Burgel, P. De Carli, Benedetta Fabrizzi, Thao Nguyen‐Khoa, Valeria Capurro, Carlo Castellani, Jean Lebihan, Karim Khoukh, Anne Guillemaut, Massimo Maschio, Laurence Weiss, Natacha Rémus, Guillaume Labbé, Julie Mankikian
article en

Abstract

N1303K-CFTR shows tissue specific correction and suboptimal response to ETI which can be improved by API.

Frontiers in PharmacologyVol. 16
Université Claude Bernard Lyon 1 (FR), Hôpital Necker-Enfants Malades (FR), Centre National de la Recherche Scientifique (FR), Université de Bordeaux (FR), Inserm (FR), Warsaw University of Life Sciences (PL), Université Paris Cité (FR), IRCCS Materno Infantile Burlo Garofolo (IT), Istituto Giannina Gaslini (IT), Martin University (US), Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico (IT), Sorbonne Université (FR), Institut Necker Enfants Malades (FR), Hôpital Armand-Trousseau (FR), Centre Hospitalier Universitaire de Besançon (FR), Hôpital Cochin (FR), Azienda Ospedaliera Universitaria Integrata Verona (IT), Vaincre la Mucoviscidose (FR), Centre Hospitalier Universitaire de Tours (FR), Assistance Publique – Hôpitaux de Paris (FR), Centre Hospitalier Régional et Universitaire de Nancy (FR), Hospices Civils de Lyon (FR), Cystic Fibrosis Research Foundation (IT), Hôpital d'Enfants (FR), Azienda Ospedaliero Universitaria Ospedali Riuniti (IT), Hôpital Pellegrin (FR), Meyer Children's Hospital (IT), Health Services and Performance Research Laboratory (FR), Hôpital Robert-Debré (FR), Institute of Biochemistry and Biophysics, Polish Academy of Sciences (PL), Centre Hospitalier Universitaire de Clermont-Ferrand (FR), Azienda Ospedaliera Universitaria Policlinico "G. Martino" (IT), Institut Cochin (FR), Hôpital des Enfants (FR), Telethon Institute Of Genetics And Medicine (IT), Istituti di Ricovero e Cura a Carattere Scientifico (IT), Centre de Recherche Cardio-Thoracique de Bordeaux (FR), Hôpital Foch (FR), Research on healthcare performance (FR), University of Brescia (IT), University of Genoa (IT), KU Leuven (BE)
American Breast Cancer Foundation, Ministero della Salute, Fondazione per la Ricerca sulla Fibrosi Cistica
Openalex Percentile: Top 53%
Atrial Fibrillation Management and Outcomes
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