Preferences for gene therapy in Duchenne muscular dystrophy: insights from patient and caregiver interviews and attribute development
This study identified the treatment characteristics most important to DMD patients and their caregivers and translated them into six key attributes with corresponding levels. It underscores the practical value of qualitative research and patient engagement in ensuring that attributes and level development for future quantitative preference elicitation studies remain clinically relevant and aligned with patient priorities.
Authors
- Lauren Van Haesendonck
- Severine A.R.A. Vermeire (ORCID: https://orcid.org/0000-0001-9942-3019)
- Eline van Overbeeke (ORCID: https://orcid.org/0000-0003-0073-9350)
- Thomas Desmet (ORCID: https://orcid.org/0000-0001-7630-4850)
- Steven Simoens (ORCID: https://orcid.org/0000-0002-9512-2005)
- Isabelle Huys (ORCID: https://orcid.org/0000-0002-4738-8298)
Institutions
- Vlerick Business School (BE)
- KU Leuven (BE)
Publication Details
- Journal
- Frontiers in Pharmacology
- Published
- 2025-09-29
- DOI
- https://doi.org/10.3389/fphar.2025.1662586
- Primary Topic
- Muscle Physiology and Disorders
- Type
- article
- Field-Weighted Citation Impact
- 0.00
Funders
- KU Leuven