Pediatric acute respiratory distress syndrome in children with type I - spinal muscular atrophy: a 12-year case series
• This is the first case series describing pediatric acute respiratory distress syndrome (pARDS) in SMA-1 children, suggesting that standard pARDS treatment could be applied with achievable survival.
Authors
- Vittoria Ferrari (ORCID: https://orcid.org/0000-0002-4395-9356)
- A. Wayne Orr (ORCID: https://orcid.org/0000-0002-2377-213X)
- Tony Christian Morena (ORCID: https://orcid.org/0000-0001-6240-8464)
- Laura Pezza (ORCID: https://orcid.org/0000-0003-0311-9202)
- Orazio Genovese (ORCID: https://orcid.org/0000-0002-1989-1363)
- Giorgia Spinazzola (ORCID: https://orcid.org/0000-0001-8055-5142)
- Rita De Sanctis (ORCID: https://orcid.org/0000-0003-3202-1933)
- Enzo Picconi (ORCID: https://orcid.org/0000-0002-1808-0665)
- Marco Piastra (ORCID: https://orcid.org/0000-0002-3144-8970)
- Danièle De Luca (ORCID: https://orcid.org/0000-0002-3846-4834)
- Antonio Varone (ORCID: https://orcid.org/0000-0002-1994-6619)
- Eugenio Maria Mercuri (ORCID: https://orcid.org/0000-0002-9851-5365)
- Gabriella De Rosa (ORCID: https://orcid.org/0000-0002-8780-5105)
- Laura Marzano
- Geremia Zito Marinosci (ORCID: https://orcid.org/0000-0002-6583-3324)
- Marika Pane (ORCID: https://orcid.org/0000-0002-4851-6124)
- Roberta Onesimo (ORCID: https://orcid.org/0000-0003-3128-6657)
- Giorgio Conti (ORCID: https://orcid.org/0000-0002-8566-9365)
- Fabrizio Racca
- Alessia Tempera
- M. C. Fedele
Institutions
- Marconi University (IT)
- Agostino Gemelli University Polyclinic (IT)
- Intensive Care Society (GB)
- Centro Clinico Nemo (IT)
- Santobono Children's Hospital (IT)
- Nini Hospital (LB)
- Carlo Forlanini Hospital (IT)
- Istituti di Ricovero e Cura a Carattere Scientifico (IT)
- Azienda Ospedaliera Nazionale SS. Antonio e Biagio e Cesare Arrigo (IT)
- Catholic University of America (US)
Publication Details
- Journal
- European Journal of Pediatrics
- Published
- 2025-09-29
- DOI
- https://doi.org/10.1007/s00431-025-06464-3
- Primary Topic
- Neurogenetic and Muscular Disorders Research
- Type
- article
- Field-Weighted Citation Impact
- 0.00