Pediatric acute respiratory distress syndrome in children with type I - spinal muscular atrophy: a 12-year case series

• This is the first case series describing pediatric acute respiratory distress syndrome (pARDS) in SMA-1 children, suggesting that standard pARDS treatment could be applied with achievable survival.

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Publication Details

Journal
European Journal of Pediatrics
Published
2025-09-29
DOI
https://doi.org/10.1007/s00431-025-06464-3
Primary Topic
Neurogenetic and Muscular Disorders Research
Type
article
Field-Weighted Citation Impact
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article

Pediatric acute respiratory distress syndrome in children with type I - spinal muscular atrophy: a 12-year case series

Vittoria Ferrari, A. Wayne Orr, Tony Christian Morena, Laura Pezza et al.
European Journal of Pediatrics
Neurogenetic and Muscular Disorders Research
article

Pediatric acute respiratory distress syndrome in children with type I - spinal muscular atrophy: a 12-year case series

Vittoria Ferrari, A. Wayne Orr, Tony Christian Morena, Laura Pezza, Orazio Genovese, Giorgia Spinazzola, Rita De Sanctis, Enzo Picconi, Marco Piastra, Danièle De Luca, Antonio Varone, Eugenio Maria Mercuri, Gabriella De Rosa, Laura Marzano, Geremia Zito Marinosci, Marika Pane, Roberta Onesimo, Giorgio Conti, Fabrizio Racca, Alessia Tempera, M. C. Fedele
article en

Abstract

• This is the first case series describing pediatric acute respiratory distress syndrome (pARDS) in SMA-1 children, suggesting that standard pARDS treatment could be applied with achievable survival.

European Journal of PediatricsVol. 184(10)
Marconi University (IT), Agostino Gemelli University Polyclinic (IT), Intensive Care Society (GB), Centro Clinico Nemo (IT), Santobono Children's Hospital (IT), Nini Hospital (LB), Carlo Forlanini Hospital (IT), Istituti di Ricovero e Cura a Carattere Scientifico (IT), Azienda Ospedaliera Nazionale SS. Antonio e Biagio e Cesare Arrigo (IT), Catholic University of America (US)
Openalex Percentile: Top 63%
Neurogenetic and Muscular Disorders Research
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