Efficacy and safety of risdiplam in adults with 5q-associated spinal muscular atrophy: a nationwide observational cohort study in Austria
Wolfgang N. Löscher, Matthias Baumann, Magdalena Gosk-Tomek, Anna Hotter et al.
Citations
3 citations
Journal
EClinicalMedicine
Topics
Neurogenetic and Muscular Disorders Research
Field-Weighted Citation Impact (FWCI)
4.88
article
Efficacy and safety of risdiplam in adults with 5q-associated spinal muscular atrophy: a nationwide observational cohort study in Austria
Wolfgang N. Löscher, Matthias Baumann, Magdalena Gosk-Tomek, Anna Hotter, Mika Rappold, Johannes Tröger, Eva Schernhammer, Omar Keritam, Susanne Grinzinger, Petra Müller, Dieter Langenscheidt, Günther Bernert, Hakan Çetin, Theresa Antonia Griedl, Stefan Quasthoff, Sukhvir P. Mahal, Fritz Zimprich, Julia Wanschitz, Astrid C. Erber, Jakob Rath, Corinne G.C. Horlings, Martin Krenn, Marcus Erdler, Caroline Kiss, Raffi Topakian, Gudrun Zulehner, Christian Eggers, Anna Wiesenhofer, Florian Knipp, Vera Elisabeth Adreana Kleinveld, Valeriu Gold, Thomas Waldhör, Nadine Langweil, Victoria Anna Gruber, Bernhard Fasching
article en
3 citations
Abstract
No abstract available for this paper.
Publication Tag
EClinicalMedicineVol. 88
Institutions
Johannes Kepler University of Linz (AT), Harvard University (US), Innsbruck Medical University (AT), Universität Innsbruck (AT), Medical University of Graz (AT), Paracelsus Medical University (AT), Vienna General Hospital (AT), Donauspital (AT), Landeskrankenhaus Feldkirch (AT), Klinikum Klagenfurt (AT), Klinikum Wels-Grieskirchen (AT), SBA Research (AT), Medical University of Vienna (AT)