Efficacy and safety of risdiplam in adults with 5q-associated spinal muscular atrophy: a nationwide observational cohort study in Austria

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Publication Details

Journal
EClinicalMedicine
Published
2025-09-27
DOI
https://doi.org/10.1016/j.eclinm.2025.103536
Citations
3
Primary Topic
Neurogenetic and Muscular Disorders Research
Type
article
Field-Weighted Citation Impact
4.88
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article

Efficacy and safety of risdiplam in adults with 5q-associated spinal muscular atrophy: a nationwide observational cohort study in Austria

Wolfgang N. Löscher, Matthias Baumann, Magdalena Gosk-Tomek, Anna Hotter et al.
3 citations
EClinicalMedicine
Neurogenetic and Muscular Disorders Research
4.88
article

Efficacy and safety of risdiplam in adults with 5q-associated spinal muscular atrophy: a nationwide observational cohort study in Austria

Wolfgang N. Löscher, Matthias Baumann, Magdalena Gosk-Tomek, Anna Hotter, Mika Rappold, Johannes Tröger, Eva Schernhammer, Omar Keritam, Susanne Grinzinger, Petra Müller, Dieter Langenscheidt, Günther Bernert, Hakan Çetin, Theresa Antonia Griedl, Stefan Quasthoff, Sukhvir P. Mahal, Fritz Zimprich, Julia Wanschitz, Astrid C. Erber, Jakob Rath, Corinne G.C. Horlings, Martin Krenn, Marcus Erdler, Caroline Kiss, Raffi Topakian, Gudrun Zulehner, Christian Eggers, Anna Wiesenhofer, Florian Knipp, Vera Elisabeth Adreana Kleinveld, Valeriu Gold, Thomas Waldhör, Nadine Langweil, Victoria Anna Gruber, Bernhard Fasching
article en
3 citations

Abstract

No abstract available for this paper.
EClinicalMedicineVol. 88
Johannes Kepler University of Linz (AT), Harvard University (US), Innsbruck Medical University (AT), Universität Innsbruck (AT), Medical University of Graz (AT), Paracelsus Medical University (AT), Vienna General Hospital (AT), Donauspital (AT), Landeskrankenhaus Feldkirch (AT), Klinikum Klagenfurt (AT), Klinikum Wels-Grieskirchen (AT), SBA Research (AT), Medical University of Vienna (AT)
Openalex Percentile: Top 4%
Neurogenetic and Muscular Disorders Research
4.88
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