Electrodiagnostic and Functional Biomarkers for Non‐Ambulatory Children With Late‐Onset Spinal Muscular Atrophy
Median-APB CMAP amplitude demonstrated sensitivity in capturing treatment response. A prospective study comparing nusinersen and risdiplam in a larger, clinically diverse cohort with a longer follow-up period is needed.
Authors
- Laura Johnson (ORCID: https://orcid.org/0000-0001-8985-3154)
- Durga Shah
- Mary E. Ritchey (ORCID: https://orcid.org/0000-0003-0304-9304)
- Vishva Natarajan
- Kimberly Carvell
- Subodh Verma (ORCID: https://orcid.org/0000-0002-4018-8533)
- M Ogata
- Sriharsha Sripadrao
Institutions
- Dartmouth College (US)
- Emory University (US)
- Universidad Peruana Cayetano Heredia (PE)
- Augusta University (US)
- Emory University Hospital (US)
- Emory Johns Creek Hospital (US)
- Children's Healthcare of Atlanta (US)
Publication Details
- Journal
- Muscle & Nerve
- Published
- 2025-09-23
- DOI
- https://doi.org/10.1002/mus.70030
- Primary Topic
- Neurogenetic and Muscular Disorders Research
- Type
- article
- Field-Weighted Citation Impact
- 0.00