Estimated Long-Term Durability of Valoctocogene Roxaparvovec Treatment in Male patients with Severe Hemophilia A: An Extrapolation of Clinical Data
Authors
- David Trueman (ORCID: https://orcid.org/0000-0002-7886-6467)
- Tara M. Robinson (ORCID: https://orcid.org/0000-0003-1513-707X)
- Sandra Santos (ORCID: https://orcid.org/0000-0003-0631-816X)
Institutions
- Office Of Health Economics (GB)
- BioMarin (United Kingdom) (GB)
- BioMarin (United States) (US)
Publication Details
- Journal
- Advances in Therapy
- Published
- 2025-09-23
- DOI
- https://doi.org/10.1007/s12325-025-03368-4
- Citations
- 2
- Primary Topic
- Hemophilia Treatment and Research
- Type
- article
- Field-Weighted Citation Impact
- 3.54