Network-based drug repurposing for psychiatric disorders using single-cell genomics
Neuropsychiatric disorders lack effective treatments due to a limited understanding of the underlying cellular and molecular mechanisms. To address this, we integrated population-scale single-cell genomics data and analyzed 23 cell-type-level gene regulatory networks across schizophrenia, bipolar disorder, and autism. Our analysis revealed potential druggable transcription factors co-regulating known risk genes that converge into cell-type-specific co-regulated modules. We applied graph neural networks on those modules to prioritize novel risk genes and leveraged them in a network-based drug repurposing framework to identify 220 drug molecules with the potential for targeting specific cell types. We found evidence for 37 of these drugs in reversing disorder-associated transcriptional phenotypes. Additionally, we discovered 335 drug-cell quantitative trait loci (eQTLs), revealing genetic variation's influence on drug target expression at the cell-type level. Our results provide a single-cell network medicine resource that provides potential mechanistic insights for advancing treatment options for neuropsychiatric disorders.
Authors
- Cagatay Dursun (ORCID: https://orcid.org/0000-0002-0897-7671)
- Noah Cohen Kalafut (ORCID: https://orcid.org/0000-0003-1421-0829)
- Jennifer Ja-Yoon Choi
- Mark Gerstein (ORCID: https://orcid.org/0000-0002-9746-3719)
- Daifeng Wang (ORCID: https://orcid.org/0000-0001-9190-3704)
- Declan Clarke (ORCID: https://orcid.org/0000-0002-6128-7485)
- Yan Xia (ORCID: https://orcid.org/0000-0001-6432-9911)
- Saniya Khullar (ORCID: https://orcid.org/0000-0002-4166-874X)
- Kalpana Hanthanan Arachchilage (ORCID: https://orcid.org/0000-0002-0849-9534)
- Chirag Gupta (ORCID: https://orcid.org/0000-0002-6121-7065)
- Xiao Zhou (ORCID: https://orcid.org/0000-0002-8933-444X)
Institutions
- University of Wisconsin–Madison (US)
- Yale University (US)
- University of Wisconsin Health (US)
Publication Details
- Journal
- Cell Genomics
- Published
- 2025-09-23
- DOI
- https://doi.org/10.1016/j.xgen.2025.101003
- Citations
- 4
- Primary Topic
- Single-cell and spatial transcriptomics
- Type
- article
- Field-Weighted Citation Impact
- 3.22