Treatment Outcome of Risdiplam and Onasemnogene Abeparvovec in an Infant With Spinal Muscular Atrophy Dependent on Prolonged Invasive Ventilation
SKHT and FSW have received consultancy fees from Novartis, Roche and Biogen for advisory boards and talks. SKHT is site PI and FSW is on study team for STEER study NCT05089656. The data that support the findings of this study are available from the corresponding author upon reasonable request.
Authors
- S K Tay (ORCID: https://orcid.org/0000-0002-3077-4184)
- Furene Sijia Wang (ORCID: https://orcid.org/0000-0003-3641-0549)
- J. Lee
- Huixin Huang
Institutions
- National University of Singapore (SG)
- National University Health System (SG)
Publication Details
- Journal
- Journal of Paediatrics and Child Health
- Published
- 2025-09-18
- DOI
- https://doi.org/10.1111/jpc.70199
- Primary Topic
- Neurogenetic and Muscular Disorders Research
- Type
- article
- Field-Weighted Citation Impact
- 0.00