Outcomes of idebenone therapy for Leber hereditary optic neuropathy in a cohort of patients from Wales
The present cohort demonstrates evidence of CRR in a high proportion of patients reaching 27 months of treatment. Further follow-up and a larger cohort of patients will provide further insight into the real-world efficacy of idebenone in LHON.
Authors
- Marcela Votruba (ORCID: https://orcid.org/0000-0002-7680-9135)
- Francis Sanders (ORCID: https://orcid.org/0000-0003-1625-7487)
Institutions
- University Hospital of Wales (GB)
- Cardiff University (GB)
Publication Details
- Journal
- Eye
- Published
- 2025-09-17
- DOI
- https://doi.org/10.1038/s41433-025-03993-x
- Primary Topic
- Drug-Induced Ocular Toxicity
- Type
- article
- Field-Weighted Citation Impact
- 0.00