Effects of Tafamidis Meglumine on Transient Focal Neurological Episodes and Meningeal Contrast Enhancement in Hereditary Transthyretin‐Related Meningeal Amyloidosis: Report of Two Patients Carrying the c.265T>C (p.Y89H) Variant
Tafamidis had a partial effect on TFNEs and meningeal contrast enhancement on MRI; however, cerebellar ataxia and cognitive decline continued to progress.
Authors
- Yasuko Kuroha
- Atsushi Ishiyama (ORCID: https://orcid.org/0000-0003-2555-212X)
- Tetsuya Takahashi (ORCID: https://orcid.org/0000-0002-3934-0219)
- N. Saito (ORCID: https://orcid.org/0009-0008-6096-1889)
- Takayoshi Tokutake (ORCID: https://orcid.org/0000-0002-6952-4908)
- Arika Hasegawa
- Takahiro Wakasugi
Institutions
- Nishi Niigata Chuo National Hospital (JP)
Publication Details
- Journal
- Brain and Behavior
- Published
- 2025-09-01
- DOI
- https://doi.org/10.1002/brb3.70856
- Primary Topic
- Amyloidosis: Diagnosis, Treatment, Outcomes
- Type
- article
- Field-Weighted Citation Impact
- 0.00