A New Staging System for Hereditary Transthyretin Amyloidosis in the Era of Specific Amyloidosis Therapies

We propose a novel staging system for ATTRv patients on specific treatment, based on two biological markers and one echocardiographic parameter, common in clinical practice.

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Publication Details

Journal
ESC Heart Failure
Published
2025-09-03
DOI
https://doi.org/10.1002/ehf2.15414
Primary Topic
Amyloidosis: Diagnosis, Treatment, Outcomes
Type
article
Field-Weighted Citation Impact
0.00

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article

A New Staging System for Hereditary Transthyretin Amyloidosis in the Era of Specific Amyloidosis Therapies

Gabriela Neculae, Benoît Funalot, Robert Adam, Ruxandra Jurcuţ et al.
ESC Heart Failure
Amyloidosis: Diagnosis, Treatment, Outcomes
article

A New Staging System for Hereditary Transthyretin Amyloidosis in the Era of Specific Amyloidosis Therapies

Gabriela Neculae, Benoît Funalot, Robert Adam, Ruxandra Jurcuţ, Daniel Coriu, Mounira Kharoubi, Amira Zaroui, Thibaud Damy
article en

Abstract

We propose a novel staging system for ATTRv patients on specific treatment, based on two biological markers and one echocardiographic parameter, common in clinical practice.

ESC Heart FailureVol. 12(6)
Inserm (FR), Carol Davila University of Medicine and Pharmacy (RO), Université Paris-Est Créteil (FR), Centre Hospitalier Universitaire Henri-Mondor (FR), Department of Health and Aged Care (AU), Institutul de Urgenţă pentru Boli Cardiovasculare "Prof.Dr. C.C. Iliescu" (RO), Amyloidosis Foundation (US), Hôpitaux Universitaires Henri-Mondor (FR), Institut Mondor de Recherche Biomédicale (FR), Institutul Clinic Fundeni (RO)
Pfizer
Openalex Percentile: Top 79%
Amyloidosis: Diagnosis, Treatment, Outcomes
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