Allogeneic haematopoietic stem cell transplantation for severe Still’s disease: a retrospective report of three paediatric patients
Allogeneic HSCT can be an effective salvage therapy in patients with refractory sJIA. However, the risk of post-transplant endothelial complications and severe inflammation in previously affected organs, such as joints, skin and lungs deserves particular attention.
Authors
- Laureline Berteloot (ORCID: https://orcid.org/0000-0001-9681-3142)
- Bénédicte Neven (ORCID: https://orcid.org/0000-0001-8941-0935)
- Paul Bastard (ORCID: https://orcid.org/0000-0002-5926-8437)
- Jade Cognard (ORCID: https://orcid.org/0000-0002-1255-7522)
- Christine Piètrement (ORCID: https://orcid.org/0000-0002-3234-5105)
- Despina Moshous (ORCID: https://orcid.org/0000-0001-6719-3693)
- Alice Hadchouel (ORCID: https://orcid.org/0000-0001-7451-9890)
- Laurye-Anne Eveillard (ORCID: https://orcid.org/0000-0003-1896-4097)
- Romain Lévy (ORCID: https://orcid.org/0000-0002-6393-0198)
- Véronique Hentgen (ORCID: https://orcid.org/0000-0003-1788-1898)
- Martin Castelle (ORCID: https://orcid.org/0000-0001-9087-4411)
- Marie‐Louise Frémond (ORCID: https://orcid.org/0000-0002-2798-9141)
- A. Welfringer‐Morin (ORCID: https://orcid.org/0000-0001-7479-3689)
- Marwa Chbihi (ORCID: https://orcid.org/0000-0002-2771-851X)
- Marie Pouletty
- Benjamin Fournier (ORCID: https://orcid.org/0000-0003-4383-7524)
- Pierre Quartier (ORCID: https://orcid.org/0000-0002-1769-549X)
- Muriel Schmutz
Institutions
- Hôpital Necker-Enfants Malades (FR)
- Université Paris Cité (FR)
- Centre de Référence Déficits Immunitaires Héréditaires (FR)
- Sorbonne Paris Cité (FR)
- Centre de Référence des Maladies Autoinflammatoires et des Amyloses (FR)
- Centre Hospitalier Universitaire de Reims (FR)
- Hôpital des Enfants (FR)
- Université de Reims Champagne-Ardenne (FR)
Publication Details
- Journal
- Lara D. Veeken
- Published
- 2025-08-25
- DOI
- https://doi.org/10.1093/rheumatology/keaf416
- Primary Topic
- Autoimmune and Inflammatory Disorders Research
- Type
- article
- Field-Weighted Citation Impact
- 0.00